Zobrazeno 1 - 10
of 320
pro vyhledávání: '"Giermasz AS"'
Autor:
Andrew D. Leavitt, Johnny Mahlangu, Priyanka Raheja, Emily Symington, Doris V. Quon, Adam Giermasz, Maria Fernanda López Fernández, Gili Kenet, Gillian Lowe, Nigel S. Key, Carolyn M. Millar, Steven W. Pipe, Bella Madan, Sheng-Chieh Chou, Robert Klamroth, Jane Mason, Hervé Chambost, Flora Peyvandi, Elaine Majerus, Dominic Pepperell, Christine Rivat, Hua Yu, Tara M. Robinson, Margareth C. Ozelo
Publikováno v:
Research and Practice in Thrombosis and Haemostasis, Vol 8, Iss 8, Pp 102615- (2024)
Background: Valoctocogene roxaparvovec, an adeno-associated virus-mediated gene therapy for severe hemophilia A, enables endogenous factor (F)VIII expression and provides bleed protection. Objectives: Determine valoctocogene roxaparvovec durability,
Externí odkaz:
https://doaj.org/article/001816e90c524b2c8af3b06f1a36444f
Autor:
Leavitt, Andrew D., Mahlangu, Johnny, Raheja, Priyanka, Symington, Emily, Quon, Doris V., Giermasz, Adam, López Fernández, Maria Fernanda, Kenet, Gili, Lowe, Gillian, Key, Nigel S., Millar, Carolyn M., Pipe, Steven W., Madan, Bella, Chou, Sheng-Chieh, Klamroth, Robert, Mason, Jane, Chambost, Hervé, Peyvandi, Flora, Majerus, Elaine, Pepperell, Dominic, Rivat, Christine, Yu, Hua, Robinson, Tara M., Ozelo, Margareth C.
Publikováno v:
In Research and Practice in Thrombosis and Haemostasis November 2024 8(8)
Autor:
Leavitt, Andrew D., Konkle, Barbara A., Stine, Kimo C., Visweshwar, Nathan, Harrington, Thomas J., Giermasz, Adam, Arkin, Steven, Fang, Annie, Plonski, Frank, Yver, Anne, Ganne, Florence, Agathon, Delphine, Resa, Maria de los Angeles, Tseng, Li-Jung, Di Russo, Gregory, Cockroft, Bettina M., Cao, Liching, Rupon, Jeremy
Publikováno v:
In Blood 29 February 2024 143(9):796-806
Autor:
O’Mahony, Brian, Dunn, Amy L., Leavitt, Andrew D., Peyvandi, Flora, Ozelo, Margareth C., Mahlangu, Johnny, Peerlinck, Kathelijne, Wang, Jiaan-Der, Lowe, Gillian C., Tan, Chee Wee, Giermasz, Adam, Tran, Huyen, Khoo, Teh-Liane, Cockrell, Erin, Pepperell, Dominic, Chambost, Hervé, López Fernández, Maria Fernanda, Kazmi, Rashid, Majerus, Elaine, Skinner, Mark W., Klamroth, Robert, Quinn, Jennifer, Yu, Hua, Wong, Wing Yen, Robinson, Tara M., Pipe, Steven W.
Publikováno v:
In Journal of Thrombosis and Haemostasis December 2023 21(12):3450-3462
Autor:
von Drygalski, Annette, Gomez, Esteban, Giermasz, Adam, Castaman, Giancarlo, Key, Nigel S., Lattimore, Susan U., Leebeek, Frank W. G., Miesbach, Wolfgang A., Recht, Michael, Gut, Robert, Dolmetsch, Ricardo, Monahan, Paul E., Le Quellec, Sandra, Pipe, Steven W.
Publikováno v:
In Blood Advances 10 October 2023 7(19):5671-5679
Autor:
Rosen, Steffen 1, Tiefenbacher, Stefan 2, Robinson, Mary 2, Huang, Mei 3, Srimani, Jaydeep 3, Mackenzie, Donnie 3, Christianson, Terri 3, Pasi, K. John 4, Rangarajan, Savita 5, Symington, Emily 6, Giermasz, Adam 7, Pierce, Glenn F. 8, Kim, Benjamin 3, Zoog, Stephen J. 3, Vettermann, Christian 3
Publikováno v:
In Blood 26 November 2020 136(22):2524-2534
Akademický článek
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Autor:
Von Drygalski, Annette, Giermasz, Adam, Castaman, Giancarlo, Key, Nigel S., Lattimore, Susan, Leebeek, Frank W.G., Miesbach, Wolfgang, Recht, Michael, Long, Alison, Gut, Robert, Sawyer, Eileen K., Pipe, Steven W.
Publikováno v:
In Blood Advances 12 November 2019 3(21):3241-3247
Akademický článek
Tento výsledek nelze pro nepřihlášené uživatele zobrazit.
K zobrazení výsledku je třeba se přihlásit.
K zobrazení výsledku je třeba se přihlásit.
Autor:
Annette Von Drygalski, Adam Giermasz, Giancarlo Castaman, Nigel S. Key, Susan Lattimore, Frank W.G. Leebeek, Wolfgang Miesbach, Michael Recht, Alison Long, Robert Gut, Eileen K. Sawyer, Steven W. Pipe
Publikováno v:
Blood Advances, Vol 3, Iss 21, Pp 3241-3247 (2019)
Etranacogene dezaparvovec (AMT-061) is a recombinant AAV5 vector including a gene cassette containing the factor IX (FIX) Padua variant under the control of a liver-specific promoter. A phase 2b study was conducted to confirm that a single dose of 2
Externí odkaz:
https://doaj.org/article/66cb66c72e9147b78eee95d74a7a1df4