Zobrazeno 1 - 10
of 1 491
pro vyhledávání: '"Giermasz AS"'
Autor:
Andrew D. Leavitt, Johnny Mahlangu, Priyanka Raheja, Emily Symington, Doris V. Quon, Adam Giermasz, Maria Fernanda López Fernández, Gili Kenet, Gillian Lowe, Nigel S. Key, Carolyn M. Millar, Steven W. Pipe, Bella Madan, Sheng-Chieh Chou, Robert Klamroth, Jane Mason, Hervé Chambost, Flora Peyvandi, Elaine Majerus, Dominic Pepperell, Christine Rivat, Hua Yu, Tara M. Robinson, Margareth C. Ozelo
Publikováno v:
Research and Practice in Thrombosis and Haemostasis, Vol 8, Iss 8, Pp 102615- (2024)
Background: Valoctocogene roxaparvovec, an adeno-associated virus-mediated gene therapy for severe hemophilia A, enables endogenous factor (F)VIII expression and provides bleed protection. Objectives: Determine valoctocogene roxaparvovec durability,
Externí odkaz:
https://doaj.org/article/001816e90c524b2c8af3b06f1a36444f
Publikováno v:
Blood Adv
Etranacogene dezaparvovec (AMT-061) is a recombinant AAV5 vector including a gene cassette containing the factor IX (FIX) Padua variant under the control of a liver-specific promoter. A phase 2b study was conducted to confirm that a single dose of 2
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::fa5beb673a4b27eb0d72ab33bb80ddc1
https://doi.org/10.1182/bloodadvances.2020002987
https://doi.org/10.1182/bloodadvances.2020002987
Publikováno v:
Blood advances [Blood Adv] 2020 Aug 11; Vol. 4 (15), pp. 3668.
Autor:
Leavitt, Andrew D. 1, ∗, Mahlangu, Johnny 2, Raheja, Priyanka 3, Symington, Emily 4, Quon, Doris V. 5, Giermasz, Adam 6, López Fernández, Maria Fernanda 7, Kenet, Gili 8, Lowe, Gillian 9, Key, Nigel S. 10, Millar, Carolyn M. 11, 12, Pipe, Steven W. 13, Madan, Bella 14, Chou, Sheng-Chieh 15, Klamroth, Robert 16, 17, Mason, Jane 18, 19, Chambost, Hervé 20, Peyvandi, Flora 21, 22, Majerus, Elaine 23, Pepperell, Dominic 24, Rivat, Christine 25, Yu, Hua 25, Robinson, Tara M. 25, Ozelo, Margareth C. 26
Publikováno v:
In Research and Practice in Thrombosis and Haemostasis November 2024 8(8)
Autor:
Leavitt, Andrew D., Konkle, Barbara A., Stine, Kimo C., Visweshwar, Nathan, Harrington, Thomas J., Giermasz, Adam, Arkin, Steven, Fang, Annie, Plonski, Frank, Yver, Anne, Ganne, Florence, Agathon, Delphine, Resa, Maria de los Angeles, Tseng, Li-Jung, Di Russo, Gregory, Cockroft, Bettina M., Cao, Liching, Rupon, Jeremy
Publikováno v:
In Blood 29 February 2024 143(9):796-806
Autor:
O’Mahony, Brian, Dunn, Amy L., Leavitt, Andrew D., Peyvandi, Flora, Ozelo, Margareth C., Mahlangu, Johnny, Peerlinck, Kathelijne, Wang, Jiaan-Der, Lowe, Gillian C., Tan, Chee Wee, Giermasz, Adam, Tran, Huyen, Khoo, Teh-Liane, Cockrell, Erin, Pepperell, Dominic, Chambost, Hervé, López Fernández, Maria Fernanda, Kazmi, Rashid, Majerus, Elaine, Skinner, Mark W., Klamroth, Robert, Quinn, Jennifer, Yu, Hua, Wong, Wing Yen, Robinson, Tara M., Pipe, Steven W.
Publikováno v:
In Journal of Thrombosis and Haemostasis December 2023 21(12):3450-3462
Autor:
von Drygalski, Annette, Gomez, Esteban, Giermasz, Adam, Castaman, Giancarlo, Key, Nigel S., Lattimore, Susan U., Leebeek, Frank W. G., Miesbach, Wolfgang A., Recht, Michael, Gut, Robert, Dolmetsch, Ricardo, Monahan, Paul E., Le Quellec, Sandra, Pipe, Steven W.
Publikováno v:
In Blood Advances 10 October 2023 7(19):5671-5679
Autor:
Dunn A; Nationwide Children's Hospital and The Ohio State University College of Medicine, Columbus, Ohio, USA., Dargaud Y; Université Lyon, Lyon, France., Abajas Y; Hemophilia and Thrombosis Center, University of North Carolina at Chapel Hill, Chapel Hill, North Carolina, USA., Carcao M; The Hospital for Sick Children, Toronto, Ontario, Canada., Castaman G; Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy., Giermasz A; University of California, Davis, Sacramento, California, USA., Hermans C; Cliniques Saint-Luc, Université Catholique de Louvain, Brussels, Belgium., Jiménez-Yuste V; Hospital Universitario La Paz, Madrid, Spain., Lewandowska M; Indiana Hemophilia and Thrombosis Center, Indianapolis, Indiana, USA., Mahlangu J; Hemophilia Comprehensive Care Center, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa., Meeks S; Emory University and Aflac Cancer and Blood Disorders Center of Children's Healthcare of Atlanta, Atlanta, Georgia, USA., Miesbach W; Goethe University Hospital, Frankfurt, Germany., Recht M; Pediatric Hematology/Oncology, Yale University School of Medicine, New Haven, Connecticut, USA., Salinas V; Center for Inherited Blood Disorders, Orange, California, USA., Chrisentery-Singleton T; American Thrombosis and Hemostasis Network, Rochester, New York, USA., Bonzo D; LFB-USA, Inc., Framingham, Massachusetts, USA., Mitchell IS; HEMA Biologics, LLC, Louisville, Kentucky, USA., Wilkinson TA; GLOVAL LLC, Broomfield, Colorado, USA., Young G; Children's Hospital Los Angeles, Los Angeles, California, USA.; Keck School of Medicine, University of Southern California, Los Angeles, California, USA.
Publikováno v:
Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2024 Dec 15. Date of Electronic Publication: 2024 Dec 15.
Autor:
Rosen, Steffen 1, Tiefenbacher, Stefan 2, Robinson, Mary 2, Huang, Mei 3, Srimani, Jaydeep 3, Mackenzie, Donnie 3, Christianson, Terri 3, Pasi, K. John 4, Rangarajan, Savita 5, Symington, Emily 6, Giermasz, Adam 7, Pierce, Glenn F. 8, Kim, Benjamin 3, Zoog, Stephen J. 3, Vettermann, Christian 3
Publikováno v:
In Blood 26 November 2020 136(22):2524-2534
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