Zobrazeno 1 - 8
of 8
pro vyhledávání: '"George Jeha"'
Autor:
Carlos Bacino, Ravi Savarirayan, William Wilcox, Paul Harmatz, John Phillips, Lynda Polgreen, Louise Tofts, Keiichi Ozono, Paul Arundel, Melita Irving, Donald Basel, Michael Bober, Joel Charrow, Hiroshi Mochizuki, Yumiko Kotani, Howard Saal, George Jeha, Lynn Han, Elena Fisheleva, Alice Huntsman-Labed, Jonathan Day
Publikováno v:
Genetics in Medicine Open, Vol 1, Iss 1, Pp 100118- (2023)
Externí odkaz:
https://doaj.org/article/4ef74f3924c244c6a347e82de79a2678
Autor:
Yulan Qi, Alice Huntsman-Labed, Carlos A. Bacino, Keiichi Ozono, Jonathan Day, Klaus Mohnike, Melita Irving, William R. Wilcox, Anu Cherukuri, Ming Liang Chan, Julie Hoover-Fong, Elena Fisheleva, William A. Horton, Kevin Larimore, Ravi Savarirayan, Lori Seid, Kala Jayaram, Joshua Henshaw, George Jeha
Publikováno v:
Clinical Pharmacokinetics. 61:263-280
Vosoritide, an analog of C-type natriuretic peptide, has been developed for the treatment of children with achondroplasia. The pharmacokinetics of vosoritide and relationships between plasma exposure and efficacy, biomarkers, and safety endpoints wer
Autor:
Ravi Savarirayan, Melita Irving, Paul Harmatz, Borja Delgado, William R. Wilcox, John Philips, Natalie Owen, Carlos A. Bacino, Louise Tofts, Joel Charrow, Lynda E. Polgreen, Julie Hoover-Fong, Paul Arundel, Ignacio Ginebreda, Howard M. Saal, Donald Basel, Rosendo Ullot Font, Keiichi Ozono, Michael B. Bober, Valerie Cormier-Daire, Kim-Hanh Le Quan Sang, Genevieve Baujat, Yasemin Alanay, Frank Rutsch, Daniel Hoernschemeyer, Klaus Mohnike, Hiroshi Mochizuki, Asako Tajima, Yumiko Kotani, David D. Weaver, Klane K. White, Clare Army, Kevin Larrimore, Keith Gregg, George Jeha, Claire Milligan, Elena Fisheleva, Alice Huntsman-Labed, Jonathan Day
This study was undertaken to collect baseline growth parameters in children with achondroplasia who might enroll in interventional trials of vosoritide, and to establish a historical control.In this prospective, observational study, participants (≤
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f453eff204de636d775f291695fcb1b7
https://hdl.handle.net/10668/22253
https://hdl.handle.net/10668/22253
Autor:
Ravi Savarirayan, William W Wilcox, Paul Harmatz, John Phillips III, Lynda E Polgreen, Louise Tofts, Keiichi Ozono, Paul Arundel, Melita Irving, Carlos A Bacino, Donald Basel, Michael B Bober, Joel Charrow, Hiroshi Mochizuki, Yumiko Kotani, Howard M Saal, George Jeha, Lynn Han, Elena Fisheleva, Alice Huntsman-Labed, Jonathan Day
Publikováno v:
Journal of the Endocrine Society. 6:A591-A592
Background Vosoritide increases annualized growth velocity (AGV) in children with achondroplasia aged 5 to 18 years. This global, phase 2, randomized, double-blind, placebo-controlled study evaluated the safety and efficacy of vosoritide on growth in
Autor:
Melita Irving, Julie Hoover-Fong, Carlos Bacino, Joel Charrow, Valérie Cormier-Daire, Lynda Polgreen, Paul Harmatz, Patricia Dickson, Michael Bober, Klaus Mohnike, William Wilcox, Alice Huntsman Labed, Sue Lawrinson, Elena Fisheleva, George Jeha, Jonathan Day, John Phillips, Ravi Savarirayan
Publikováno v:
Genetics in Medicine. 24:S352-S353
Autor:
Anu Cherukuri, Ming Liang Chan, Alice Huntsman Labed, Kala Jayaram, Kim Hanh Le Quan Sang, Carlos A. Bacino, Joel Charrow, Kevin Larimore, George Jeha, Jonathan Day, Natalie N. Owen, Bret L. Bostwick, Ravi Savarirayan, Valérie Cormier-Daire, Julie Hoover-Fong, Melita Irving, Paul Harmatz, Patricia I. Dickson, John A. Phillips
Publikováno v:
Yearbook of Paediatric Endocrinology.
Achondroplasia is a genetic disorder that inhibits endochondral ossification, resulting in disproportionate short stature and clinically significant medical complications. Vosoritide is a biologic analogue of C-type natriuretic peptide, a potent stim
Autor:
Melita Irving, Valérie Cormier-Daire, Paul Harmatz, Patricia I. Dickson, Elena Fisheleva, Joel Charrow, Julie Hoover-Fong, John D. Phillips, Kala Jayaram, Alice Huntsman Labed, Ravi Savarirayan, Jonathan Day, Lynda E. Polgreen, George Jeha, Carlos A. Bacino, Kevin Larimore
Publikováno v:
Web of Science
Autor:
William Maixner, Jonathan Day, Dominic Thompson, Melita Irving, Marcin Kronhardt, Amaka C. Offiah, Elena Fisheleva, Ashok Raghavan, James Powell, Daniel J. A. Connolly, George Jeha, Ravi Savarirayan, Sajda Ghani
Publikováno v:
Science Progress. 104:003685042110037
Achondroplasia causes narrowing of the foramen magnum and the spinal canal leading to increased mortality due to cervicomedullary compression in infants and significant morbidity due to spinal stenosis later in adulthood. Vosoritide is a C-natriureti