Zobrazeno 1 - 10
of 168 580
pro vyhledávání: '"Genetic vectors."'
Autor:
Potter RA; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Moeller IH; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Khan S; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Haegel H; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Hollenstein A; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Steiner G; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Wandel C; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Murphy AP; Roche Products Ltd, Welwyn Garden City, UK., Asher DR; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Palatinsky E; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Griffin DA; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Mason S; Sarepta Therapeutics, Inc., Cambridge, MA, USA., Iannaccone ST; Departments of Pediatrics and Neurology, University of Texas Southwestern Medical Center and Children's Health, Dallas, TX, USA., Zaidman CM; Department of Neurology, Washington University in St. Louis, St. Louis, MO, USA., Rodino-Klapac LR; Sarepta Therapeutics, Inc., Cambridge, MA, USA. LRodinoKlapac@Sarepta.com.
Publikováno v:
Scientific reports [Sci Rep] 2025 Jan 02; Vol. 15 (1), pp. 4. Date of Electronic Publication: 2025 Jan 02.
Autor:
Link EK; Ludwig-Maximilians-University Munich (LMU Munich), Department of Veterinary Sciences, Division of Virology, Oberschleißheim, Germany., Tscherne A; Ludwig-Maximilians-University Munich (LMU Munich), Department of Veterinary Sciences, Division of Virology, Oberschleißheim, Germany., Sutter G; Ludwig-Maximilians-University Munich (LMU Munich), Department of Veterinary Sciences, Division of Virology, Oberschleißheim, Germany., Smith ER; Brighton Collaboration, A Program of the Task Force for Global Health, Decatur, GA, USA. Electronic address: bc-coordinator@taskforce.org., Gurwith M; Brighton Collaboration, A Program of the Task Force for Global Health, Decatur, GA, USA., Chen RT; Brighton Collaboration, A Program of the Task Force for Global Health, Decatur, GA, USA., Volz A; University of Veterinary Medicine Hannover, Institute of Virology, Hannover, Germany.
Publikováno v:
Vaccine [Vaccine] 2025 Jan 01; Vol. 43 (Pt 1), pp. 126521. Date of Electronic Publication: 2024 Nov 28.
Autor:
Stitz J; Research Group Medical Biotechnology & Bioengineering, Faculty of Applied Natural Sciences, TH Köln - University of Applied Sciences, Campusplatz 1, 51379, Leverkusen, Germany. Electronic address: joern.stitz@th-koeln.de.
Publikováno v:
Virology [Virology] 2025 Jan; Vol. 602, pp. 110300. Date of Electronic Publication: 2024 Nov 14.
Autor:
Rossetti E; Janssen Vaccines & Prevention, Leiden, The Netherlands., Vujadinovic M; Janssen Vaccines & Prevention, Leiden, The Netherlands., van Huizen E; Janssen Vaccines & Prevention, Leiden, The Netherlands., Tolboom J; Janssen Vaccines & Prevention, Leiden, The Netherlands., Schuitemaker H; Janssen Vaccines & Prevention, Leiden, The Netherlands., Yao F; Brigham and Women's Hospital, Boston, MA, United States of America., Zahn R; Janssen Vaccines & Prevention, Leiden, The Netherlands., Saeland E; Janssen Vaccines & Prevention, Leiden, The Netherlands.
Publikováno v:
PloS one [PLoS One] 2024 Dec 31; Vol. 19 (12), pp. e0310250. Date of Electronic Publication: 2024 Dec 31 (Print Publication: 2024).
Autor:
Furusho T; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Das R; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Hakui H; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Sairavi A; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Adachi K; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Galbraith-Liss MS; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Rajagopal P; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Horikawa M; Dotter Department of Interventional Radiology, Oregon Health & Science University School of Medicine, Portland, OR, USA., Luo S; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Li L; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA., Yamada K; Dotter Department of Interventional Radiology, Oregon Health & Science University School of Medicine, Portland, OR, USA., Andeen N; Department of Pathology, Oregon Health & Science University School of Medicine, Portland, OR, USA., Dissen GA; Division of Neuroscience, Oregon National Primate Research Center, Oregon Health & Science University, Beaverton, OR, USA.; Molecular Virology Core, Oregon National Primate Research Center, Oregon Health & Science University, Beaverton, OR, USA., Nakai H; Department of Molecular and Medical Genetics, Oregon Health & Science University School of Medicine, Portland, OR, USA. nakaih@ohsu.edu.; Division of Neuroscience, Oregon National Primate Research Center, Oregon Health & Science University, Beaverton, OR, USA. nakaih@ohsu.edu.; Department of Molecular Microbiology and Immunology, Oregon Health & Science University School of Medicine, Portland, OR, USA. nakaih@ohsu.edu.
Publikováno v:
Nature communications [Nat Commun] 2024 Dec 30; Vol. 15 (1), pp. 10728. Date of Electronic Publication: 2024 Dec 30.
Autor:
Yang K; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China; College of Materials and Chemical Engineering, Hunan Institute of Engineering, Xiangtan, Hunan 411104 , China. Electronic address: kanyang@shsmu.edu.cn., Li T; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China., Geng Y; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China., Zhang R; College of Materials and Chemical Engineering, Hunan Institute of Engineering, Xiangtan, Hunan 411104 , China., Xu Z; College of Materials and Chemical Engineering, Hunan Institute of Engineering, Xiangtan, Hunan 411104 , China., Wu J; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China., Yuan Y; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China., Zhang Y; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China., Qiu Z; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China. Electronic address: qiuzilong@shsmu.edu.cn., Li F; Department of Developmental and Behavioural Pediatric & Child Primary Care, Brain and Behavioural Research Unit of Shanghai Institute for Pediatric Research and MOE-Shanghai Key Laboratory for Children's Environmental Health of Xinhua Hospital & Songjiang Research Institute, Shanghai Jiao Tong University School of Medicine, Shanghai 200092, China. Electronic address: feili@shsmu.edu.cn.
Publikováno v:
STAR protocols [STAR Protoc] 2024 Dec 20; Vol. 5 (4), pp. 103344. Date of Electronic Publication: 2024 Sep 25.
Autor:
Günaydin C; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA., Sondhi D; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA., Kaminsky SM; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA., Lephart HC; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA., Leopold PL; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA., Hackett NR; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA., Khanna R; LEXEO Therapeutics, New York, NY, USA., Crystal RG; Department of Genetic Medicine, Weill Cornell Medical College, New York, NY, USA. Electronic address: geneticmedicine@med.cornell.edu.
Publikováno v:
Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Dec 04; Vol. 32 (12), pp. 4303-4318. Date of Electronic Publication: 2024 Nov 06.
Autor:
Lam P; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH 43215, USA., Zygmunt DA; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH 43215, USA., Ashbrook A; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH 43215, USA., Yan C; Department of Pathology and Laboratory Medicine, Indiana University School of Medicine, Indianapolis, IN 46202, USA., Du H; Department of Pathology and Laboratory Medicine, Indiana University School of Medicine, Indianapolis, IN 46202, USA., Martin PT; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH 43215, USA; Department of Pediatrics, The Ohio State University School of Medicine, Columbus, OH 43210, USA. Electronic address: paul.martin@nationwidechildrens.org.
Publikováno v:
Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Dec 04; Vol. 32 (12), pp. 4272-4284. Date of Electronic Publication: 2024 Oct 28.
Autor:
Wang JH; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA; Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia; Ophthalmology, Department of Surgery, University of Melbourne, East Melbourne, VIC 3002, Australia., Zhan W; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA; Department of Medicine, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA 01605, USA., Gallagher TL; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA., Gao G; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA 01605, USA. Electronic address: guangping.gao@umassmed.edu.
Publikováno v:
Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Dec 04; Vol. 32 (12), pp. 4185-4207. Date of Electronic Publication: 2024 Oct 28.
Autor:
Li C; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA. Electronic address: cli1239@uw.edu., Georgakopoulou A; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA., Paschoudi K; Gene and Cell Therapy Center, Hematology Department, George Papanicolaou Hospital, Thessaloniki, Greece., Anderson AK; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA., Huang L; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA., Gil S; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA., Giannaki M; Second Department of Internal Medicine, School of Medicine, Aristotle University of Thessaloniki, Thessaloniki, Greece., Vlachaki E; Second Department of Internal Medicine, School of Medicine, Aristotle University of Thessaloniki, Thessaloniki, Greece., Newby GA; Merkin Institute of Transformative Technologies in Healthcare, Broad Institute of MIT and Harvard, Cambridge, MA, USA; Department of Chemistry and Chemical Biology, Harvard University, Cambridge, MA, USA; Howard Hughes Medical Institute, Harvard University, Cambridge, MA, USA; Johns Hopkins University, Department of Genetic Medicine, Baltimore, MD, USA., Liu DR; Merkin Institute of Transformative Technologies in Healthcare, Broad Institute of MIT and Harvard, Cambridge, MA, USA; Department of Chemistry and Chemical Biology, Harvard University, Cambridge, MA, USA; Howard Hughes Medical Institute, Harvard University, Cambridge, MA, USA., Yannaki E; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA; Gene and Cell Therapy Center, Hematology Department, George Papanicolaou Hospital, Thessaloniki, Greece., Kiem HP; Stem and Gene Therapy Program, Fred Hutchinson Cancer Research Center, Seattle, WA 98109, USA., Lieber A; University of Washington, Department of Medicine, Division of Medical Genetics, Seattle, WA 98195, USA; University of Washington, Department of Laboratory Medicine and Pathology, Seattle, WA 98195, USA.
Publikováno v:
Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Dec 04; Vol. 32 (12), pp. 4353-4371. Date of Electronic Publication: 2024 Oct 28.