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pro vyhledávání: '"GT Group"'
Autor:
MC Ozelo, AD Leavitt, J Mahlangu, G Kenet, SW Pipe, S Chou, R Klamroth, F Peyvandi, T Robinson, GT Group
Publikováno v:
Hematology, Transfusion and Cell Therapy, Vol 46, Iss , Pp S573-S574 (2024)
Objectives: Valoctocogene roxaparvovec (AAV5-hFVIII-SQ), a gene transfer therapy for severe hemophilia A, enables endogenous factor VIII (FVIII) production to prevent bleeding. We present efficacy and safety outcomes 4-years post-valoctocogene roxapa
Externí odkaz:
https://doaj.org/article/2556db0b03f64027bd8f9cb620b1972d
