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Akademický článek

GENETIC AND NON-GENETIC DETERMINANTS OF SUCCESSFUL IMMUNE TOLERANCE INDUCTION IN PEOPLE WITH SEVERE HEMOPHILIA A

Publikováno v: Hematology, Transfusion and Cell Therapy, Vol 46, Iss , Pp S562-S563 (2024)

Background: Eradicating inhibitors to restore the effectiveness of Factor VIII (FVIII) is a desirable treatment goal for People with Severe Hemophilia A (PwSHA) and inhibitors, as this enables treatment of bleeding episodes with FVIII concentrates. H

Externí odkaz: https://doaj.org/article/9a14647d2e784f2e9ac3886aafab9e62

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Akademický článek

LARGE DELETIONS IN THE F8 GENE PREDICT IMMUNE TOLERANCE INDUCTION FAILURE IN PEOPLE WITH SEVERE HEMOPHILIA A

Publikováno v: Hematology, Transfusion and Cell Therapy, Vol 46, Iss , Pp S564- (2024)

Immune Tolerance Induction (ITI) is the only treatment to eradicate inhibitors in people with Severe Hemophilia A (SHA). Successful ITI restores Factor VIII (FVIII) tolerance. ITI is demanding and successful in approximately 70% of people. Therefore,

Externí odkaz: https://doaj.org/article/8a4854d5cc734792892446f0a32e01ce

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Akademický článek

TREATMENT SATISFACTION AND JOINT HEALTH OUTCOMES WITHIN A REAL-WORLD HAEMOPHILIA B POPULATION: THE ADELPHI DISEASE SPECIFIC PROGRAMMESURVEY

Autor: V Jiméne-ZYuste, C Percier, T Porstmann, N Ball, G Castaman, GG Fabbron, MGA Okuma

Publikováno v: Hematology, Transfusion and Cell Therapy, Vol 46, Iss , Pp S569-S570 (2024)

Background: While haemophilia care continues to improve, People with Haemophilia B (PwHB) may still experience disease and treatment burden. Aims: To describe physician-reported treatment satisfaction and joint health outcomes in a real-world populat

Externí odkaz: https://doaj.org/article/65b106869d46482781180cf05da4dfec

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