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pro vyhledávání: '"Fritz Hull"'
Autor:
Robert N. Plasschaert, Mark P. DeAndrade, Fritz Hull, Quoc Nguyen, Tara Peterson, Aimin Yan, Mariana Loperfido, Cristina Baricordi, Luigi Barbarossa, John K. Yoon, Yildirim Dogan, Zeenath Unnisa, Jeffrey W. Schindler, Niek P. van Til, Luca Biasco, Chris Mason
Publikováno v:
Molecular Therapy. 30:3209-3225
Hematopoietic stem/progenitor cell gene therapy (HSPC-GT) has shown clear neurological benefit in rare diseases, which is achieved through the engraftment of genetically modified microglia-like cells (MLCs) in the brain. Still, the engraftment dynami
Genetically engineered microglia-like cells have therapeutic potential for neurodegenerative disease
Autor:
Luigi Barbarossa, Niek P. van Til, Tara Peterson, Cristina Baricordi, Christopher E. Mason, Robert N. Plasschaert, Zeenath Unnisa, Mariana Loperfido, Jeffrey W. Schindler, Aimin Yan, Fritz Hull, Yildirim Dogan, Mark P. DeAndrade, John K. Yoon, Luca Biasco, Quoc Nguyen
Hematopoietic stem/progenitor cell gene therapy (HSPC-GT) results in the engraftment of genetically modified microglia-like cells (MLCs) in the brain. While HSPC-GT has shown a clear neurological benefit in the clinic for specific rare diseases, the
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::1f54bc3f10bedc2465a41f5e0e4cb191
https://doi.org/10.1101/2021.09.16.460703
https://doi.org/10.1101/2021.09.16.460703