Zobrazeno 1 - 10
of 20
pro vyhledávání: '"Frances Male"'
Autor:
Charles C. Berry, Christopher Nobles, Emmanuelle Six, Yinghua Wu, Nirav Malani, Eric Sherman, Anatoly Dryga, John K. Everett, Frances Male, Aubrey Bailey, Kyle Bittinger, Mary J. Drake, Laure Caccavelli, Paul Bates, Salima Hacein-Bey-Abina, Marina Cavazzana, Frederic D. Bushman
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 4, Iss C, Pp 17-26 (2017)
Analysis of sites of newly integrated DNA in cellular genomes is important to several fields, but methods for analyzing and visualizing these datasets are still under development. Here, we describe tools for data analysis and visualization that take
Externí odkaz:
https://doaj.org/article/f6f59b94b4594769ac2569d51c8c88e1
Autor:
Eric Sherman, Christopher Nobles, Charles C. Berry, Emmanuelle Six, Yinghua Wu, Anatoly Dryga, Nirav Malani, Frances Male, Shantan Reddy, Aubrey Bailey, Kyle Bittinger, John K. Everett, Laure Caccavelli, Mary J. Drake, Paul Bates, Salima Hacein-Bey-Abina, Marina Cavazzana, Frederic D. Bushman
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 4, Iss C, Pp 39-49 (2017)
Integration of new DNA into cellular genomes mediates replication of retroviruses and transposons; integration reactions have also been adapted for use in human gene therapy. Tracking the distributions of integration sites is important to characteriz
Externí odkaz:
https://doaj.org/article/3427f2d0dfcc4d91928bb6ad271ea637
Autor:
Amit Sharma, Alison Slaughter, Nivedita Jena, Lei Feng, Jacques J Kessl, Hind J Fadel, Nirav Malani, Frances Male, Li Wu, Eric Poeschla, Frederic D Bushman, James R Fuchs, Mamuka Kvaratskhelia
Publikováno v:
PLoS Pathogens, Vol 10, Iss 5, p e1004171 (2014)
The quinoline-based allosteric HIV-1 integrase (IN) inhibitors (ALLINIs) are promising candidates for clinically useful antiviral agents. Studies using these compounds have highlighted the role of IN in both early and late stages of virus replication
Externí odkaz:
https://doaj.org/article/7ceda5ee2d6f497c8ecf7da87f9b4d83
Autor:
Josiah Petersen, Mary Jane Drake, Emily A Bruce, Amber M Riblett, Chukwuka A Didigu, Craig B Wilen, Nirav Malani, Frances Male, Fang-Hua Lee, Frederic D Bushman, Sara Cherry, Robert W Doms, Paul Bates, Kenneth Briley
Publikováno v:
PLoS Pathogens, Vol 10, Iss 2, p e1003911 (2014)
The Bunyaviridae comprise a large family of RNA viruses with worldwide distribution and includes the pathogenic New World hantavirus, Andes virus (ANDV). Host factors needed for hantavirus entry remain largely enigmatic and therapeutics are unavailab
Externí odkaz:
https://doaj.org/article/f0959b3fb26345a8ad77874cb23e408f
Autor:
Matthew J Pace, Erin H Graf, Luis M Agosto, Angela M Mexas, Frances Male, Troy Brady, Frederic D Bushman, Una O'Doherty
Publikováno v:
PLoS Pathogens, Vol 8, Iss 7, p e1002818 (2012)
Despite the effectiveness of highly active antiretroviral therapy (HAART) in treating individuals infected with HIV, HAART is not a cure. A latent reservoir, composed mainly of resting CD4+T cells, drives viral rebound once therapy is stopped. Unders
Externí odkaz:
https://doaj.org/article/dbccde35766d4ad09774f366e3f2ac9f
Autor:
Christine Rivat, Ronjon Chakraverty, Emma C. Morris, Alan D. Salama, Anne Galy, H. Bobby Gaspar, Karen F. Buckland, Adrian J. Thrasher, Ronnie Chee, Rita Tendeiro, Sarita Workman, Thomas A. Fox, Siobhan O. Burns, Frederick D. Bushman, Kimberly Gilmour, Frances Male, Katie Butler, Cecile Duret, Sarah Grace, Katie Snell, Fulvio Mavilio, Hazem Ibrahim, Havinder Hara
Publikováno v:
Blood
Blood, 2017, 130 (11), pp.1327-1335. ⟨10.1182/blood-2017-04-777136⟩
Blood, American Society of Hematology, 2017, 130 (11), pp.1327-1335. ⟨10.1182/blood-2017-04-777136⟩
Blood, 2017, 130 (11), pp.1327-1335. ⟨10.1182/blood-2017-04-777136⟩
Blood, American Society of Hematology, 2017, 130 (11), pp.1327-1335. ⟨10.1182/blood-2017-04-777136⟩
International audience; Until recently, hematopoietic stem cell transplantation was the only curative option for Wiskott-Aldrich syndrome (WAS). The first attempts at gene therapy for WAS using a Upsilon-retroviral vector improved immunological param
Autor:
Anatoly Dryga, Emmanuelle Six, Yinghua Wu, Mary Jane Drake, Christopher L. Nobles, Eric J. Sherman, Aubrey Bailey, Laure Caccavelli, Nirav Malani, Paul Bates, Salima Hacein-Bey-Abina, Frances Male, Frederic D. Bushman, Shantan Reddy, Marina Cavazzana, Charles C. Berry, John K. Everett, Kyle Bittinger
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 4, Iss C, Pp 39-49 (2017)
Molecular Therapy. Methods & Clinical Development
Sherman, E; Nobles, C; Berry, CC; Six, E; Wu, Y; Dryga, A; et al.(2017). INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular Genomes. MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 4, 39-49. doi: 10.1016/j.omtm.2016.11.002. UC San Diego: Retrieved from: http://www.escholarship.org/uc/item/2tq50500
Molecular Therapy. Methods & Clinical Development
Sherman, E; Nobles, C; Berry, CC; Six, E; Wu, Y; Dryga, A; et al.(2017). INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular Genomes. MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 4, 39-49. doi: 10.1016/j.omtm.2016.11.002. UC San Diego: Retrieved from: http://www.escholarship.org/uc/item/2tq50500
Integration of new DNA into cellular genomes mediates replication of retroviruses and transposons; integration reactions have also been adapted for use in human gene therapy. Tracking the distributions of integration sites is important to characteriz
Autor:
Troy Brady, Benjamin M. Dyer, Emile Johann Velthuisen, Nirav Malani, Kushol Gupta, Jerry Jeffrey, Gregory D. Van Duyne, Young Hwang, Liping Wang, Frances Male, Robert T. Nolte, Frederic D. Bushman
Publikováno v:
Journal of Biological Chemistry. 289:20477-20488
HIV-1 replication in the presence of antiviral agents results in evolution of drug-resistant variants, motivating the search for additional drug classes. Here we report studies of GSK1264, which was identified as a compound that disrupts the interact
Autor:
Nirav Malani, Aubrey Bailey, Kyle Bittinger, Salima Hacein-Bey-Abina, Frances Male, Marina Cavazzana, Charles C. Berry, Laure Caccavelli, Frederic D. Bushman, Mary Jane Drake, Emmanuelle Six, Yinghua Wu, Paul Bates, Christopher L. Nobles, Eric J. Sherman, Anatoly Dryga, John K. Everett
Publikováno v:
Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 4, Iss C, Pp 17-26 (2017)
Berry, CC; Nobles, C; Six, E; Wu, Y; Malani, N; Sherman, E; et al.(2017). INSPIIRED: Quantification and Visualization Tools for Analyzing Integration Site Distributions. MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 4, 17-26. doi: 10.1016/j.omtm.2016.11.003. UC San Diego: Retrieved from: http://www.escholarship.org/uc/item/1z88x22p
Molecular Therapy: Methods & Clinical Development, Vol 4, Iss C, Pp 17-26 (2017)
Berry, CC; Nobles, C; Six, E; Wu, Y; Malani, N; Sherman, E; et al.(2017). INSPIIRED: Quantification and Visualization Tools for Analyzing Integration Site Distributions. MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 4, 17-26. doi: 10.1016/j.omtm.2016.11.003. UC San Diego: Retrieved from: http://www.escholarship.org/uc/item/1z88x22p
Analysis of sites of newly integrated DNA in cellular genomes is important to several fields, but methods for analyzing and visualizing these datasets are still under development. Here, we describe tools for data analysis and visualization that take
Autor:
Fabien Touzot, Gregory Hopkins, Sung-Yun Pai, Salima Hacein-Bey-Abina, Frances Male, Myriam Armant, Despina Moshous, Luigi D. Notarangelo, David A. Williams, Jerome Ritz, Capucine Picard, Helen de Boer, Annick Lim, Karen F. Buckland, Dongjing Guo, Axel Schambach, Laure Caccavelli, Johannes C.M. Van der Loo, Satiro N. De Oliveira, Leslie Lehmann, Punam Malik, Alexandra H. Filipovich, Johanna Blondeau, M. Angélica Marinovic, Stéphane Blanche, Kit L. Shaw, Charles C. Berry, Alla V. Tsytsykova, Karen S. Fernandez, Alain Fischer, Eric A. Sherman, Anne Marie McNicol, Leslie E. Silberstein, Guilhem Cros, Adrian J. Thrasher, Bénédicte Neven, H. Bobby Gaspar, Frederic D. Bushman, Matias Oleastro, Nirav Malani, Marina Cavazzana, Donald B. Kohn, Jack J. Bleesing, Christine Rivat, Wendy B. London, Chad E. Harris, Christopher Baum, Emmanuelle Six, Jinhua Xu-Bayford
Publikováno v:
Hacein-Bey-Abina, S; Pai, SY; Gaspar, HB; Armant, M; Berry, CC; Blanche, S; et al.(2014). A modified γ-retrovirus vector for X-linked severe combined immunodeficiency. New England Journal of Medicine, 371(15), 1407-1417. doi: 10.1056/NEJMoa1404588. UCLA: Retrieved from: http://www.escholarship.org/uc/item/2bn9c1nt
BACKGROUND In previous clinical trials involving children with X-linked severe combined immunodeficiency (SCID-X1), a Moloney murine leukemia virus–based γ-retrovirus vector expressing interleukin-2 receptor γ-chain (γc) complementary DNA succes
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::96c2567d602f6e62c57cf31b5a1d09c6
https://europepmc.org/articles/PMC4274995/
https://europepmc.org/articles/PMC4274995/