Multicenter expanded access program for access to investigational products for amyotrophic lateral sclerosis.

Autor: Neel DV; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Baselga-Garriga C; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Benson M; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Keegan M; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Chase M; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., D'Agostino D; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Drake K; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Hagar JL; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Hasenoehrl MG; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Kulesa-Kelley J; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Leite A; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Mohapatra S; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Portaro SM; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Pothier LM; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Rosenthal J; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Sherman AV; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Yu H; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., McCaffrey A; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Ho D; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Luppino S; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Bedlack R; Department of Neurology, Duke University, Durham, North Carolina, USA., Heitzman D; MDA/ALS Clinic, Texas Neurology, Dallas, Texas, USA., Ajroud-Driss S; Les Turner ALS Center, Northwestern University, Chicago, Illinois, USA., Katz J; California Pacific Medical Center Research Institute and Forbes Norris MDA/ALS Research and Treatment Center, San Francisco, California, USA., Felice K; Department of Neuromuscular Medicine, Hospital for Special Care, New Britain, Connecticut, USA., Whitaker C; Department of Neuromuscular Medicine, Hospital for Special Care, New Britain, Connecticut, USA., Ladha S; Gregory W. Fulton ALS and Neuromuscular Center, Barrow Neurological Institute, Phoenix, Arizona, USA., Alameda G; Holy Cross Hospital, Silver Spring, Maryland, USA., Locatelli E; Center for Collaborative Research, Nova Southeastern University and Dr. Kiran C. Patel College of Allopathic Medicine, Fort Lauderdale, Florida, USA., Qureshi IA; Biohaven Pharmaceuticals, Inc., New Haven, Connecticut, USA., Hotchkin MT; Clene Nanomedicine, Inc., Salt Lake, Utah, USA., Hayden MR; Naarden, Prilenia Therapeutics, The Netherlands.; Center for Molecular Medicine and Therapeutics, British Columbia Children's Hospital Research Institute, University of British Columbia, Vancouver, British Columbia, Canada., Cudkowicz ME; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Babu S; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Berry JD; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Paganoni S; Sean M. Healey and AMG Center for ALS and the Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA.; Spaulding Rehabilitation Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Publikováno v: Muscle & nerve [Muscle Nerve] 2024 Aug; Vol. 70 (2), pp. 232-239. Date of Electronic Publication: 2024 Jun 06.

Correction to: A double-blind, placebo-controlled, randomized trial of PXT3003 for the treatment of Charcot-Marie-Tooth type 1A.

Autor: Attarian S; Reference Center for Neuromuscular Disorders and ALS, CHU La Timone, Marseille, France. Shahram.ATTARIAN@ap-hm.fr., Young P; Department of Neurology, Medical Park Bad Feilnbach, Bad Feilnbach, Germany., Brannagan TH; Columbia University Medical Center, The Neurological Institute, New York, USA., Adams D; French Reference Center for Rare Peripheral Neuropathies, Service de Neurologie Adulte, APHP, CHU Bicêtre, Le Kremlin Bicêtre, France., Van Damme P; Department of Neurology, University Hospitals Leuven, KU, Leuven, Belgium.; Center for Brain & Disease Research, VIB, Leuven, Belgium., Thomas FP; Department of Neurology, Hackensack University Medical Center, Hackensack, USA.; Department of Neurology, Saint Louis University School of Medicine, St. Louis, USA., Casanovas C; Neuromuscular Unit, Neurology Department, Bellvitge University Hospital, Barcelona, Spain.; Neurometabolic Diseases Group, Bellvitge Research Institute (IDIBELL) and CIBERER, Barcelona, Spain., Kafaie J; Department of Neurology, Saint Louis University School of Medicine, St. Louis, USA., Tard C; U1171, Centre de référence des maladies neuromusculaires Nord Est Ile de France, Hôpital Salengro CHU de Lille, Lille, France., Walter MC; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany., Péréon Y; Centre de Référence Maladies Neuromusculaires AOC, Filnemus, Euro-NMD, CHU Nantes, Hôtel-Dieu, Nantes, France., Walk D; Clinical Neuroscience Research Unit, University of Minnesota, Minneapolis, USA., Stino A; University of Michigan Health System, Ann Arbor, MI, USA., de Visser M; Department of Neurology, Amsterdam University Medical Centres, University of Amsterdam, Amsterdam Neuroscience, Amsterdam, The Netherlands., Verhamme C; Department of Neurology, Amsterdam University Medical Centres, University of Amsterdam, Amsterdam Neuroscience, Amsterdam, The Netherlands., Amato A; Department of Neurology, Brigham and Women's Hospital, Boston, USA., Carter G; St. Luke's Rehabilitation Institute, Physical Medicine and Rehabilitation, Spokane, USA., Magy L; CHU Dupuytren, Limoges, France., Statland JM; University of Kansas Medical Center, Kansas City, USA., Felice K; Department of Neuromuscular Medicine, Hospital for Special Care, New Britain, USA.

Publikováno v: Orphanet journal of rare diseases [Orphanet J Rare Dis] 2024 Apr 01; Vol. 19 (1), pp. 142. Date of Electronic Publication: 2024 Apr 01.

A Novel Remote Patient and Medication Monitoring Solution to Improve Adherence and Persistence With Inflammatory Bowel Disease Therapy (ASSIST Study): Protocol for a Randomized Controlled Trial.

Autor: Axelrad J; Division of Gastroenterology, Department of Medicine, NYU Grossman School of Medicine, New York, NY, United States., Long M; Division of Gastroenterology and Hepatology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, NC, United States., Horst S; Division of Gastroenterology, Hepatology, and Nutrition, Department of Medicine, Vanderbilt University School of Medicine, Nashville, TN, United States., Afzali A; Division of Gastroenterology, Department of Medicine, University of Cincinnati College of Medicine, Cincinnati, OH, United States., Sapir T; Synchronyx, Boca Raton, FL, United States., Fajardo K; Synchronyx, Boca Raton, FL, United States., De Felice K; Division of Gastroenterology, Department of Medicine, University of Cincinnati College of Medicine, Cincinnati, OH, United States., Sandler R; Division of Gastroenterology and Hepatology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, NC, United States., Cross R; Division of Gastroenterology, Department of Medicine, University of Maryland School of Medicine, Baltimore, MD, United States.

Publikováno v: JMIR research protocols [JMIR Res Protoc] 2022 Dec 15; Vol. 11 (12), pp. e40382. Date of Electronic Publication: 2022 Dec 15.

Systematic review: colitis associated with anti- CTLA-4 therapy.

Autor: Gupta, A.¹, De Felice, K. M.², Loftus, E. V.², Khanna, S.²

Publikováno v: Alimentary Pharmacology & Therapeutics. Aug2015, Vol. 42 Issue 4, p406-417. 12p. 2 Color Photographs, 1 Diagram, 3 Charts.

Lip Swelling as Initial Presentation of Crohn's Disease.

Autor: Nowakowski H; Louisiana State University, Department of Gastroenterology, New Orleans, LA., Peyton N; Louisiana State University, Department of Gastroenterology, New Orleans, LA., De Felice K; University of Cincinnati, Department of Gastroenterology, Cincinnati, OH.

Publikováno v: Gastro hep advances [Gastro Hep Adv] 2022 Mar 15; Vol. 1 (2), pp. 251-252. Date of Electronic Publication: 2022 Mar 15 (Print Publication: 2022).