Zobrazeno 1 - 10
of 49
pro vyhledávání: '"Eugene, Schneider"'
Autor:
Nicholas J. Viney, Shuling Guo, Li‐Jung Tai, Brenda F. Baker, Mariam Aghajan, Shiangtung W. Jung, Rosie Z. Yu, Sheri Booten, Heather Murray, Todd Machemer, Sebastien Burel, Sue Murray, Gustavo Buchele, Sotirios Tsimikas, Eugene Schneider, Richard S. Geary, Merrill D. Benson, Brett P. Monia
Publikováno v:
ESC Heart Failure, Vol 8, Iss 1, Pp 652-661 (2021)
Abstract Aims Amyloidogenic transthyretin (ATTR) amyloidosis is a fatal disease characterized by progressive cardiomyopathy and/or polyneuropathy. AKCEA‐TTR‐LRx (ION‐682884) is a ligand‐conjugated antisense drug designed for receptor‐mediat
Externí odkaz:
https://doaj.org/article/3297462a8e6e4c1081fbb6040b37c72e
Autor:
John K. Diep, Rosie Z. Yu, Nicholas J. Viney, Eugene Schneider, Shuling Guo, Scott Henry, Brett Monia, Richard Geary, Yanfeng Wang
Publikováno v:
British Journal of Clinical Pharmacology. 88:5389-5398
Transthyretin-mediated amyloidosis is a progressive and fatal disease caused by the build-up of misfolded transthyretin (TTR) protein. Eplontersen is a triantennary N-acetyl galactosamine (GalNAc3)-conjugated antisense oligonucleotide targeting TTR m
Autor:
Chafic Karam, Julian Gillmore, Gengshi Chen, Nia Jenkins, Mike Hale, Gemma Taylor, Jersey Chen, Nicholas Viney, Eugene Schneider
Publikováno v:
Wednesday, April 26.
Autor:
Teresa Coelho, Márcia Waddington Cruz, Chi-Chao Chao, Yeşim Parman, Jonas Wixner, Markus Weiler, Fabio A. Barroso, Noel R. Dasgupta, Shiangtung W. Jung, Eugene Schneider, Nicholas J. Viney, P. James B. Dyck, Yukio Ando, Julian D. Gillmore, Sami Khella, Morie A. Gertz, Laura Obici, John L. Berk
Introduction: Hereditary transthyretin (ATTRv) amyloidosis is a rare, severe, progressive, debilitating, and ultimately fatal disease caused by systemic deposition of transthyretin (TTR) amyloid fibrils. ATTRv amyloidosis occurs in both males and fem
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ae5798a91e42710915de5d07acf1a118
http://urn.kb.se/resolve?urn=urn:nbn:se:umu:diva-202005
http://urn.kb.se/resolve?urn=urn:nbn:se:umu:diva-202005
Autor:
Teresa, Coelho, Márcia, Waddington Cruz, Chi-Chao, Chao, Yeşim, Parman, Jonas, Wixner, Markus, Weiler, Fabio A, Barroso, Noel R, Dasgupta, Shiangtung W, Jung, Eugene, Schneider, Nicholas J, Viney, P James B, Dyck, Yukio, Ando, Julian D, Gillmore, Sami, Khella, Morie A, Gertz, Laura, Obici, John L, Berk
Publikováno v:
Neurology and therapy.
Hereditary transthyretin (ATTRv) amyloidosis is a rare, severe, progressive, debilitating, and ultimately fatal disease caused by systemic deposition of transthyretin (TTR) amyloid fibrils. ATTRv amyloidosis occurs in both males and females. Eplonter
Autor:
Shiangtung W. Jung, Li Jung Tai, Márcia Waddington-Cruz, William J. Litchy, Sotirios Tsimikas, Peter J. Dyck, Cecilia Monteiro, Gustavo Buchele, Julian D. Gillmore, Michela Brambatti, John L. Berk, Eugene Schneider, Yukio Ando, Teresa Coelho, Morie A. Gertz, Merrill D. Benson, Nicholas J. Viney, Louis O'Dea, Richard S. Geary, Brett P. Monia, Sami Khella, Laura Obici
Publikováno v:
Neurology and therapy, vol 10, iss 1
Neurology and Therapy
Neurology and Therapy
Introduction AKCEA-TTR-LRx is a ligand-conjugated antisense (LICA) drug in development for the treatment of hereditary transthyretin amyloidosis (hATTR), a fatal disease caused by mutations in the transthyretin (TTR) gene. AKCEA-TTR-LRx shares the sa
Autor:
Kenneth Newman, Marc Riedl, Cindy Lui, Laura Bordone, Veronica Alexander, Eugene Schneider, Danny Cohn
Publikováno v:
Journal of Allergy and Clinical Immunology. 151:AB134
Autor:
Laura Bordone, Kenneth Newman, Cindy Lui, Veronica Alexander, Marc Riedl, Eugene Schneider, Danny Cohn
Publikováno v:
Journal of Allergy and Clinical Immunology. 151:AB129
Autor:
Leighla Tayefeh, Marc Riedl, Laura Bordone, Kenneth Newman, Cindy Lui, Veronica Alexander, Danny Cohn, Eugene Schneider
Publikováno v:
Journal of Allergy and Clinical Immunology. 151:AB129
Autor:
Yanfeng Wang, John K. Diep, Rosie Z. Yu, Eunju Hurh, Ewa Karwatowska‐Prokopczuk, Eugene Schneider, Scott Henry, Sanjay Bhanot, Richard S. Geary
Publikováno v:
Journal of clinical pharmacologyReferences.
The pharmacokinetics (PK) of 2'-O-methoxyethyl and phosphorothioate antisense oligonucleotides (ASOs), with or without N-acetyl galactosamine conjugation, have been well characterized following subcutaneous or intravenous drug administration. However