Zobrazeno 1 - 1
of 1
pro vyhledávání: '"Emily deLos Reyes"'
Autor:
Aryun Kim, Anita Grover, Kevin Hammon, Greg deHart, Peter Slasor, Anu Cherukuri, Temitayo Ajayi, David Jacoby, Angela Schulz, Nicola Specchio, Emily deLos Reyes, Paul Gissen, Joshua W. Henshaw
Publikováno v:
Clinical and Translational Science, Vol 14, Iss 2, Pp 635-644 (2021)
Cerliponase alfa is recombinant human tripeptidyl peptidase 1 (TPP1) delivered by i.c.v. infusion for CLN2, a pediatric neurodegenerative disease caused by deficiency in lysosomal enzyme TPP1. We report the pharmacokinetics (PK) and pharmacodynamics
Externí odkaz:
https://doaj.org/article/afb882a5970146d6bafd1acb5b2b22cf
