Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium

Autor: Thakar, Monica S ^*, Logan, Brent R, Puck, Jennifer M, Dunn, Elizabeth A, Buckley, Rebecca H, Cowan, Morton J, O'Reilly, Richard J, Kapoor, Neena, Satter, Lisa Forbes, Pai, Sung-Yun, Heimall, Jennifer, Chandra, Sharat, Ebens, Christen L, Chellapandian, Deepak, Williams, Olatundun, Burroughs, Lauri M, Saldana, Blachy Davila, Rayes, Ahmad, Madden, Lisa M, Chandrakasan, Shanmuganathan, Bednarski, Jeffrey J, II, DeSantes, Kenneth B, Cuvelier, Geoffrey D E, Teira, Pierre, Gillio, Alfred P, Eissa, Hesham, Knutsen, Alan P, Goldman, Frederick D, Aquino, Victor M, Shereck, Evan B, Moore, Theodore B, Caywood, Emi H, Lugt, Mark T Vander, Rozmus, Jacob, Broglie, Larisa, Yu, Lolie C, Shah, Ami J, Andolina, Jeffrey R, Liu, Xuerong, Parrott, Roberta E, Dara, Jasmeen, Prockop, Susan, Martinez, Caridad A, Kapadia, Malika, Jyonouchi, Soma C, Sullivan, Kathleen E, Bleesing, Jack J, Chaudhury, Sonali, Petrovic, Aleksandra, Keller, Michael D, Quigg, Troy C, Parikh, Suhag, Shenoy, Shalini, Seroogy, Christine, Rubin, Tamar, Decaluwe, Hélène, Routes, John M, Torgerson, Troy R, Leiding, Jennifer W, Pulsipher, Michael A, Kohn, Donald B, Griffith, Linda M, Haddad, Elie ^*, Dvorak, Christopher C ^*, Notarangelo, Luigi D ^*

Publikováno v: In The Lancet 8-14 July 2023 402(10396):129-140

Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC

Autor: Cuvelier, Geoffrey D.E. ^*, Logan, Brent R., Prockop, Susan E., Buckley, Rebecca H., Kuo, Caroline Y., Griffith, Linda M., Liu, Xuerong, Yip, Alison, Hershfield, Michael S., Ayoub, Paul G., Moore, Theodore B., Dorsey, Morna J., O'Reilly, Richard J., Kapoor, Neena, Pai, Sung-Yun, Kapadia, Malika, Ebens, Christen L., Forbes Satter, Lisa R., Burroughs, Lauri M., Petrovic, Aleksandra, Chellapandian, Deepak, Heimall, Jennifer, Shyr, David C., Rayes, Ahmad, Bednarski, Jeffrey J., Chandra, Sharat, Chandrakasan, Shanmuganathan, Gillio, Alfred P., Madden, Lisa, Quigg, Troy C., Caywood, Emi H., Dávila Saldaña, Blachy J., DeSantes, Kenneth, Eissa, Hesham, Goldman, Frederick D., Rozmus, Jacob, Shah, Ami J., Vander Lugt, Mark T., Thakar, Monica S., Parrott, Roberta E., Martinez, Caridad, Leiding, Jennifer W., Torgerson, Troy R., Pulsipher, Michael A., Notarangelo, Luigi D., Cowan, Morton J., Dvorak, Christopher C., Haddad, Elie, Puck, Jennifer M., Kohn, Donald B.

Publikováno v: In Blood 18 August 2022 140(7):685-705

COVID-19 Disease in Children With ALL Receiving Maintenance Therapy: Do Not Discount the Risk

Autor: Kahn, Alissa R., Davis, Elizabeth S., Dai, Chen, Caudill, Caroline V., Martinez, Isaac, Brackett, Julienne, Sharma, Archana, Schwalm, Carla, Kebede, Ann, Dickens, David S., Richman, Joshua, Colace, Susan, Araya, Brook, Bhatia, Smita, Wolfson, Julie A., Levine, Jennifer M., Johnston, Emily E., Aftandilian, Catherine, Agrawal, Anurag K., De Angulo, Guillermo, Aristizabal, Paula, Bailey, Kayleen, Bardwell, Jenna K., Becton, David L., Bemrich-Stolz, Christina J., Boal, Lauren H, Boston, Catherine W.H., Bradfield, Scott M., Caywood, Emi H., Cohn, Shannon M., Colace, Susan I., Coven, Scott L., Cramer, Stuart L., Cuglievan, Branko, Dargart, Jamie L., Daghistani, Doured, Dhir, Aditi, Dickens, David S., Dumitriu, Anca, Eslin, E., Esquilin, Jose M., Feinberg, Shari L., Ferdjallah, Asmaa, Fernandez, Karen S., Fixler, Jason, Foley, Jessica M., Gampel, Bradley H., Glasser, Chana L., Goodman, Jessica F., Gotesman, Moran, Gowans, L. Kate, Gupta, Ajay, HaDuong, Josephine H., Halpern, Steven L., Hara, Harneet K., Hartman, Lisa R., Herring, Katye L., Hesko, Caroline S., Aguayo-Hiraldo, Paibel, Hoeft, Alice K., Hu, Caroline Y., Huo, Jeffrey S., Ikeda, Alan K., Isakoff, Michael S., Jain, Akshat, Kahn, Alissa R., Kothari, Prachi D., Krajewski, Jennifer A., Kram, David E., Krystal, Julie I., Kyono, Wade T., Langevin, Mary A., Hayes-Lattin, Brandon, Law, Jason, Levine, Jennifer M, Lorenzana, Adonis Napoleon, Lotterman, Craig D., Majlessipour, Fataneh, Marri, Preethi R., Massey, Gita V., Monteleone, Philip M., Moskop, Amy M., Mowbray, Catriona, Navalkele, Pournima D., Olson, Janice F., Ostrodka, Leanne, O’suoji, Chibuzo C., Patel, Pratik A., Pawlowska, Anna, Perl, Anna Sechser, Pinchinat, Ashley E., Prasad, Pinki K., Rangaswami, Arun Atreiya, Raulji, Chittalsinh M., Rico, Juan Felipe, Saha, Aniket, Salman, Emad Kassim, SantaCruz, Nadine P., Sarangi, Susmita N., Schwalm, Carla M., Sharma, Archana, Shaw, Peter H., Simon, David C., Slayton, William B., Smith, Amy A., Smitherman, Andrew B., Sorge, Caryn E., Sun, Jessica M., Symons, Heather J., Tal, Adit, Thomas, Stefanie M., Tran, Hung C., Troutman, Jacob A., Turcotte, Lucie M., Valdez, Jessica M., Varela, Carly R., Whipple, Nicholas S., Wilkes, Jennifer J., Woods-Swafford, Wendy, Yim, Yung S., Zhang, Yaoping

Publikováno v: JCO Oncology Practice; December 2024, Vol. 20 Issue: 12 p1655-1662, 8p

Benefits and challenges with diagnosing chronic and late acute GVHD in children using the NIH consensus criteria

Autor: Cuvelier, Geoffrey D.E. ^*, Nemecek, Eneida R., Wahlstrom, Justin T., Kitko, Carrie L., Lewis, Victor A., Schechter, Tal, Jacobsohn, David A., Harris, Andrew C., Pulsipher, Michael A., Bittencourt, Henrique, Choi, Sung Won, Caywood, Emi H., Kasow, Kimberly A., Bhatia, Monica, Oshrine, Benjamin R., Flower, Allyson, Chaudhury, Sonali, Coulter, Donald, Chewning, Joseph H., Joyce, Michael, Savaşan, Süreyya, Pawlowska, Anna B., Megason, Gail C., Mitchell, David, Cheerva, Alexandra C., Lawitschka, Anita, West, Lori J., Pan, Bo, Al Hamarneh, Yazid N., Halevy, Anat, Schultz, Kirk R.

Publikováno v: In Blood 18 July 2019 134(3):304-316

Prospective PTCTC Trial of Myeloablative HaploBMT with Post-transplant Cyclophosphamide for Pediatric Acute Leukemias

Autor: Juan Carlos Fierro-Pineda, Hua-Ling Tsai, Amanda L Blackford, Andrew Cluster, Emi H Caywood, Jignesh Dalal, Jeffrey H Davis, R. Maarten Egeler, Jeffrey Huo, Michelle Hudspeth, Amy K. Keating, Susan S Kelly, Joerg Krueger, Dean A Lee, Leslie Elaine Lehmann, Lisa Madden, Benjamin R Oshrine, Michael A Pulsipher, Terry J Fry, Heather J Symons

Publikováno v: Blood Advances.

Promising results have been reported for adult patients with high-risk hematologic malignancies undergoing haploidentical bone marrow transplant (haploBMT) with post-transplantation cyclophosphamide (PTCy). We report results from the first multicente

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_________::9ea4e6f0d0b7c5850d1fe70db1cd3feb
https://doi.org/10.1182/bloodadvances.2023010281