Zobrazeno 1 - 10
of 304
pro vyhledávání: '"Ellis J, Neufeld"'
Autor:
Joseph Neumeyer, Ruei-Zeng Lin, Kai Wang, Xuechong Hong, Tien Hua, Stacy E. Croteau, Ellis J. Neufeld, Juan M. Melero-Martin
Publikováno v:
Blood Advances, Vol 3, Iss 24, Pp 4166-4176 (2019)
Abstract: Hemophilia A (HA) is a bleeding disorder caused by mutations in the F8 gene encoding coagulation factor VIII (FVIII). Current treatments are based on regular infusions of FVIII concentrates throughout a patient's life. Alternatively, viral
Externí odkaz:
https://doaj.org/article/049f5c7c1bfa4c3f92d65e81c80b301b
Autor:
Robert J Klaassen, Kristin A Shimano, Rachael F Grace, Jenny M Despotovic, Ellis J Neufeld, Carolyn M Bennett, Clement Ma, Wendy B London, Cindy Neunert
Publikováno v:
BMJ Open, Vol 11, Iss 8 (2021)
Externí odkaz:
https://doaj.org/article/8b461b4475594a1cb7c6bfb03973cae3
Autor:
Margaret V. Ragni, Guy Young, Glaivy Batsuli, Emily Bisson, Shannon L. Carpenter, Stacy E. Croteau, Adam Cuker, Randall G. Curtis, Michael Denne, Bruce Ewenstein, Amber Federizo, Neil Frick, Kerry Funkhouser, Lindsey A. George, W. Keith Hoots, Shawn M. Jobe, Emily Krava, Christopher James Langmead, Roger J. Lewis, José López, Lynn Malec, Ziva Mann, Moses E. Miles, Emma Neely, Ellis J. Neufeld, Glenn F. Pierce, Steven W. Pipe, Lisa R. Pitler, Leslie Raffini, Kathaleen M. Schnur, Jordan A. Shavit
Publikováno v:
Expert Review of Hematology. 16:107-127
Autor:
Eduard J. van Beers, Stephanie van Straaten, D. Holmes Morton, Wilma Barcellini, Stefan W. Eber, Bertil Glader, Hassan M. Yaish, Satheesh Chonat, Janet L. Kwiatkowski, Jennifer A. Rothman, Mukta Sharma, Ellis J. Neufeld, Sujit Sheth, Jenny M. Despotovic, Nina Kollmar, Dagmar Pospíšilová, Christine M. Knoll, Kevin Kuo, Yves D. Pastore, Alexis A. Thompson, Peter E. Newburger, Yaddanapudi Ravindranath, Winfred C. Wang, Marcin W. Wlodarski, Heng Wang, Susanne Holzhauer, Vicky R. Breakey, Madeleine Verhovsek, Joachim Kunz, Melissa A. McNaull, Melissa J. Rose, Heather A. Bradeen, Kathryn Addonizio, Anran Li, Hasan Al-Sayegh, Wendy B. London, Rachael F. Grace
Publikováno v:
Haematologica, Vol 104, Iss 2 (2019)
Externí odkaz:
https://doaj.org/article/7c186564490a4bcea73e25b735945c6c
Autor:
Maria Domenica Cappellini, Ali T. Taher, Antonio Piga, Farrukh Shah, Ersi Voskaridou, Vip Viprakasit, John B. Porter, Olivier Hermine, Ellis J. Neufeld, Alexis A. Thompson, Derek Tang, Aylin Yucel, Jennifer Lord‐Bessen, Peiwen Yu, Shien Guo, Jeevan K. Shetty, Dimana Miteva, Tatiana Zinger, Jay T. Backstrom, Esther Natalie Oliva
Publikováno v:
European Journal of Haematology.
Autor:
John Chapin, Alan R. Cohen, Sean Trimble, Patricia J. Giardina, Jeanne Boudreaux, Elliott Vichinsky, Kristy Kenney, Ellis J. Neufeld, Alexis A. Thompson, Binh C. Le
Publikováno v:
British Journal of Haematology. 196:380-389
Thalassaemia is caused by genetic globin defects leading to anaemia, transfusion-dependence and comorbidities. Reduced survival and systemic organ disease affect transfusion-dependent thalassaemia major and thalassaemia intermedia. Recent improvement
Autor:
Ellis J. Neufeld, Nickhill Bhakta, Nancy S. Bolous, Andrew M. Davidoff, Ulrike M. Reiss, Huiqi Wang, Carlos Rodriguez-Galindo, Amit C. Nathwani, Meenakshi Devidas, Michael M Meagher, Bryan A. Piras, Timothy W. Jacobs, Yichen Chen
Publikováno v:
Blood. 138:1677-1690
Adeno-associated virus (AAV)-mediated gene therapy is a novel treatment promising to reduce morbidity associated with hemophilia. Although multiple clinical trials continue to evaluate efficacy and safety, limited cost-effectiveness data have been pu
Autor:
Nancy S Bolous, Nidhi Bhatt, Nickhill Bhakta, Ellis J Neufeld, Andrew M Davidoff, Ulrike M Reiss
Publikováno v:
Journal of blood medicine. 13
Gene therapy for hemophilia using adeno-associated virus (AAV) derived vectors can reduce or eliminate patients' disease-related complications and improve their quality of life. Broad implementation globally will lead to societal gains and foster hea
Autor:
Tien Hua, Joseph Neumeyer, Ellis J. Neufeld, Ruei-Zeng Lin, Stacy E. Croteau, Kai Wang, Xuechong Hong, Juan M. Melero-Martin
Publikováno v:
Blood Advances. 3:4166-4176
Hemophilia A (HA) is a bleeding disorder caused by mutations in the F8 gene encoding coagulation factor VIII (FVIII). Current treatments are based on regular infusions of FVIII concentrates throughout a patient’s life. Alternatively, viral gene the
Autor:
Rachael F. Grace, Clement Ma, Wendy B. London, Cindy Neunert, Ellis J. Neufeld, Carolyn M. Bennett, Kristin A. Shimano, Jenny M. Despotovic, Robert J. Klaassen
Publikováno v:
BMJ open, vol 11, iss 8
BMJ Open
BMJ Open, Vol 11, Iss 8 (2021)
BMJ Open
BMJ Open, Vol 11, Iss 8 (2021)
IntroductionImmune thrombocytopaenia (ITP) is an acquired disorder of low platelets and risk of bleeding. Although many children can be observed until spontaneous remission, others require treatment due to bleeding or impact on health-related quality
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ada1f7f32838d70bd65160fbd94c2a48
https://escholarship.org/uc/item/9h11s5hj
https://escholarship.org/uc/item/9h11s5hj