Zobrazeno 1 - 1
of 1
pro vyhledávání: '"Elisa C. Tsao"'
Autor:
Gilles Morin, Chen-En Tsai, R. Parini, Elisa C. Tsao, Hanna Mandel, Michael Beck, Mislen Bauer, Nancy D. Leslie, Tara O’Meara, Deya Corzo, Brian W.H. Tsai, Susan M. Richards, Mikael Jokic, Daniel Gruskin, John P. Clancy, Claire Morgan, Ans T. van der Ploeg, Priya S. Kishnani
Publikováno v:
Pediatric research. 66(3)
In a previous 52-week trial, treatment with alglucosidase alfa markedly improved cardiomyopathy, ventilatory function, and overall survival among 18 children