Výsledky vyhledávání - "Eddie Darton"

Akademický článek

O19: Integrated analyses of data from clinical trials of delandistrogene moxeparvovec gene therapy in DMD

Autor: Erin O’Rourke, Crystal Proud, Craig Zaidman, Perry B. Shieh, Craig McDonald, John W. Day, Stefanie Mason, Maitea Guridi, Lixin Han, Lixi Yu, Carol Reid, Eddie Darton, Christoph Wandel, James Richardson, Jyoti Malhotra, Teji Singh, Louise Rodino-Klapac, Jerry Mendell

Publikováno v: Genetics in Medicine Open, Vol 1, Iss 1, Pp 100115- (2023)

Externí odkaz: https://doaj.org/article/3e80487af3b44c5fac8da0cba332879d

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Akademický článek

P314: Long-term safety and sustained functional benefit in patients with DMD 4 years post-treatment with delandistrogene moxeparvovec: A phase 1/2a study

Autor: Erin O’Rourke, Jerry R. Mendell, Zarife Sahenk, Kelly J. Lehman, Linda P. Lowes, Natalie F. Reash, Megan Iammarino, Lindsay Alfano, Sarah Lewis, Kathleen Church, Richard Shell, Rachael A. Potter, Danielle Griffin, Mark J. Hogan, Shufang Wang, Stefanie Mason, Eddie Darton, Louise Rodino-Klapac

Publikováno v: Genetics in Medicine Open, Vol 1, Iss 1, Pp 100342- (2023)

Externí odkaz: https://doaj.org/article/fb9e1b284811470595a4cfbc12d4ff7e

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Integrated Analyses of Data from Clinical Trials of Delandistrogene Moxeparvovec (SRP-9001) in Duchenne Muscular Dystrophy (DMD) (S48.006)

Autor: Crystal Proud, Craig Zaidman, Perry Shieh, Craig McDonald, John Day, Stefanie Mason, Maitea Guridi, Lixin Han, Lixi Yu, Carol Reid, Eddie Darton, Christoph Wandel, James Richardson, Jyoti Malhotra, Tejdip Singh, Louise Rodino-Klapac, Jerry Mendell

Publikováno v: Thursday, April 27.

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_________::5862a1d97622d0da89f4ba24e50c3523
https://doi.org/10.1212/wnl.0000000000203470

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EMBARK, a Phase 3 Trial Evaluating Safety and Efficacy of Delandistrogene Moxeparvovec (SRP- 9001) in Duchenne Muscular Dystrophy (DMD): Study Design and Baseline Characteristics (P5-8.012)

Autor: Francesco Muntoni, Eugenio Mercuri, Ulrike Schara Schmidt, Hirofumi Komaki, James Richardson, Tejdip Singh, Maitea Guridi, Stefanie Mason, Alex Murphy, Lixi Yu, Carol Reid, Eddie Darton, Christoph Wandel, Jerry Mendell

Publikováno v: Monday, April 24.

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_________::aabb3e2264ff43cdfdd694f0d140ea1b
https://doi.org/10.1212/wnl.0000000000203455

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Long-term Safety and Efficacy in Patients with DMD 4 Years Post-Treatment with Delandistrogene Moxeparvovec (SRP-9001) in a Phase 1/2a Study (P3-8.006)

Autor: Jerry Mendell, Zarife Sahenk, Kelly Lehman, Linda Lowes, Natalie Reash, Megan Iammarino, Lindsay Alfano, Sarah Lewis, Kathleen Church, Richard Shell, Rachael Potter, Danielle Griffin, Mark Hogan, Shufang Wang, Stefanie Mason, Eddie Darton, Louise Rodino-Klapac

Publikováno v: Sunday, April 23.

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_________::744f2d0475628d639ac0585d33c7a8ca
https://doi.org/10.1212/wnl.0000000000203462

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One-year Data from ENDEAVOR, a Phase 1b Trial of Delandistrogene Moxeparvovec (SRP-9001) in Patients with Duchenne Muscular Dystrophy (DMD) (S48.003)

Autor: Craig Zaidman, Crystal Proud, Craig McDonald, Stefanie Mason, Maitea Guridi, Shufang Wang, Carol Reid, Eddie Darton, Christoph Wandel, Sarah Lewis, Jyoti Malhotra, Danielle Griffin, Rachael Potter, Louise Rodino-Klapac, Jerry Mendell

Publikováno v: Thursday, April 27.

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_________::56a750a48d983e3a398aec8ce6c363de
https://doi.org/10.1212/wnl.0000000000203475

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