Zobrazeno 1 - 4
of 4
pro vyhledávání: '"Dominique Cross"'
Autor:
Dominique Cross, Kathleen A. Marshall, Sarah McCague, Katherine A. High, Satha Thill, Daniel C. Chung, Zi-Fan Yu, Jennifer Wellman, Julie DiStefano-Pappas, Jean Bennett
Publikováno v:
Clinical & Experimental Ophthalmology. 46:247-259
Importance This novel endpoint tracks functional vision changes in patients with inherited retinal dystrophies (IRDs) over time. Background The aims of the study were to determine whether a multi-luminance mobility test (MLMT) can detect functional v
Autor:
Xiaosong Zhu, Jean Bennett, Chris A. Johnson, Katie Wachtel, Jean Walshire, Zi Fan Yu, Julie Pappas, Taylor Kehoe, Elliott H. Sohn, Jennifer Wellman, Vinit B. Mahajan, Bart P. Leroy, Michelle T. Weckmann, Francesca Simonelli, Okan U. Elci, Dominique Cross, Amy Tillman, J. Fraser Wright, Lindsey A. George, Kathleen A. Marshall, Julia A. Haller, Maria C. Davis, Edwin M. Stone, Janet Wittes, Laura E. Dingfield, Dina Y. Gewaily, Sarah McCague, Leslie Raffini, Katherine A. High, Albert M. Maguire, Hannah Reichert, Arlene V. Drack, Daniel C. Chung, Wanda Pfeifer, F. Parker Hudson, Stephen R. Russell
Publikováno v:
The Lancet. 390:849-860
Background Phase 1 studies have shown potential benefit of gene replacement in RPE65-mediated inherited retinal dystrophy. This phase 3 study assessed the efficacy and safety of voretigene neparvovec in participants whose inherited retinal dystrophy
Autor:
Daniel C, Chung, Sarah, McCague, Zi-Fan, Yu, Satha, Thill, Julie, DiStefano-Pappas, Jean, Bennett, Dominique, Cross, Kathleen, Marshall, Jennifer, Wellman, Katherine A, High
Publikováno v:
Clinicalexperimental ophthalmology. 46(3)
IMPORTANCE: This novel endpoint tracks functional vision changes in patients with inherited retinal dystrophies (IRDs) over time. BACKGROUND: The aims of the study were to determine whether a multi-luminance mobility test (MLMT) can detect functional
Autor:
Alberto Auricchio, Katherine A. High, Julie DiStefano-Pappas, Kathleen A. Marshall, Dominique Cross, J. Fraser Wright, Albert M. Maguire, Puya Aravand, Okan U. Elci, Sarah McCague, Federico Mingozzi, Laura Cyckowski, Bart P. Leroy, Daniel C. Chung, Jennifer Wellman, Jason Ruggiero, Francesca Simonelli, Eric A. Pierce, Junwei Sun, Manzar Ashtari, Jeannette L. Bennicelli, Jean Bennett
Publikováno v:
LANCET
LANCET, 2016, 388 (10045), pp.661-72. ⟨10.1016/S0140-6736(16)30371-3⟩
The Lancet
The Lancet, 2016, 388 (10045), pp.661-72. ⟨10.1016/S0140-6736(16)30371-3⟩
LANCET, 2016, 388 (10045), pp.661-72. ⟨10.1016/S0140-6736(16)30371-3⟩
The Lancet
The Lancet, 2016, 388 (10045), pp.661-72. ⟨10.1016/S0140-6736(16)30371-3⟩
International audience; BACKGROUND: Safety and efficacy have been shown in a phase 1 dose-escalation study involving a unilateral subretinal injection of a recombinant adeno-associated virus (AAV) vector containing the RPE65 gene (AAV2-hRPE65v2) in i
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f9adfa71eeaec8bb5fe1e821d109f2c2
http://hdl.handle.net/11591/358419
http://hdl.handle.net/11591/358419