Zobrazeno 1 - 3
of 3
pro vyhledávání: '"Daniel Takefman"'
Autor:
Johannes C.M. Van der Loo, Jerome M. Teitel, Benjamin J. Samelson-Jones, Adam Cuker, Xavier M. Anguela, Marcus E. Carr, Catherine E. McGuinn, Yifeng Chen, Linda B. Couto, Adam Giermasz, Suvankar Majumdar, Katie Wachtel, Jonathan M. Ducore, Stefan Tiefenbacher, Margaret V. Ragni, J. Fraser Wright, Olga Zelenaia, Katherine A. High, Yun Liu, John E.J. Rasko, Daniel Takefman, Lisa M. Sullivan, Angela Winters, Daniel Hui, Alvin Luk, Spencer K. Sullivan, Valder R. Arruda, Lindsey A. George
Publikováno v:
The New England journal of medicine. 377(23)
The prevention of bleeding with adequately sustained levels of clotting factor, after a single therapeutic intervention and without the need for further medical intervention, represents an important goal in the treatment of hemophilia.We infused a si
Autor:
Daniel Takefman, Lilia Bi
Publikováno v:
Gene and Cell Therapy ISBN: 9781466571990
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::f259387f510bbe6459fc43db86305a77
https://doi.org/10.1201/b18002-59
https://doi.org/10.1201/b18002-59
Autor:
Katie Wachtel, Marcus E. Carr, Katherine A. High, Lisa M. Sullivan, Spencer K. Sullivan, Adam Giermasz, Yifeng Chen, Aline M. Galvão, Linda B. Couto, Alvin Luk, J. Fraser Wright, Jerome M. Teitel, Jonathan M. Ducore, Daniel J. Hui, Adam Cuker, Xavier M. Anguela, Catherine E. McGuinn, Suvankar Majumdar, Daniel Takefman, Lindsey A. George, Teresa Urich
Publikováno v:
Blood. 128:3-3
Background: Earlier data demonstrated long-term expression of factor IX (mean FIX:C ~5.1%) following AAV8-mediated gene transfer at 2 x1012 vg/kg in hemophilia B (Nathwani et al., 2014). While the clinical improvement imparted by stable FIX levels is