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pro vyhledávání: '"Dan Elwell"'
Autor:
Roland W. Herzog, Edmund Y Yang, Melissa Burton, Timothy C. Nichols, Katherine A. High, Gary J. Kurtzman, Marjorie S. Read, Dwight A. Bellinger, Dan Elwell, Paul A. Fields, Linda B. Couto, Kenneth M. Brinkhous, J. Nathan Hagstrom, Gregory M. Podsakoff
Publikováno v:
Nature Medicine. 5:56-63
Hemophilia B is a severe X-linked bleeding diathesis caused by the absence of functional blood coagulation factor IX, and is an excellent candidate for treatment of a genetic disease by gene therapy. Using an adeno-associated viral vector, we demonst