Zobrazeno 1 - 10
of 25
pro vyhledávání: '"D. Scaglioni"'
Autor:
Volker Straub, Jennifer E. Morgan, Thomas Voit, Valeria Ricotti, Laurent Servais, Joana Domingos, Jan J.G.M. Verschuuren, L. Phillips, Imelda J. M. de Groot, Francesco Muntoni, Pierpaolo Ala, V. Selby, Andreea Mihaela Seferian, Erik H. Niks, D. Scaglioni, Yvonne D. Krom, F. Catapano, K. Maresh
Publikováno v:
Epigenomics, 12, 1899-1915
Epigenomics, 12, 21, pp. 1899-1915
Epigenomics, 12(21), 1899-1915. FUTURE MEDICINE LTD
Epigenomics, 12, 21, pp. 1899-1915
Epigenomics, 12(21), 1899-1915. FUTURE MEDICINE LTD
Item does not contain fulltext Aim: To perform cross-sectional and longitudinal miRNA profiling in plasma from Duchenne muscular dystrophy (DMD) subjects and find non-invasive biomarkers in DMD. Subjects/materials & methods: Plasma was collected from
Autor:
D. Scaglioni, Matthew Ellis, F. Catapano, Francesco Muntoni, Lucy Feng, D. Chambers, Caroline Sewry, Rahul Phadke, Jennifer E. Morgan, Silvia Torelli
Publikováno v:
Acta Neuropathologica Communications, Vol 8, Iss 1, Pp 1-16 (2020)
Acta Neuropathologica Communications
Acta Neuropathologica Communications
The primary molecular endpoint for many Duchenne muscular dystrophy (DMD) clinical trials is the induction, or increase in production, of dystrophin protein in striated muscle. For accurate endpoint analysis, it is essential to have reliable, robust
Autor:
F. Catapano, Jennifer E. Morgan, Caroline Sewry, Matthew Ellis, D. Scaglioni, Erica Koenig, Matthew Beck, Mauro Monforte, Lucy Feng, Volker Straub, Francesco Muntoni, Silvia Torelli, Eugenio Mercuri, D. Chambers, Jyoti Malhotra, Linda Popplewell, Shawn Harriman, Laurent Servais, Michela Guglieri, Rahul Phadke
Publikováno v:
Acta Neuropathologica Communications
Acta Neuropathologica Communications, Vol 9, Iss 1, Pp 1-17 (2021)
Acta Neuropathologica Communications, Vol 9, Iss 1, Pp 1-17 (2021)
During the last decade, multiple clinical trials for Duchenne muscular dystrophy (DMD) have focused on the induction of dystrophin expression using different strategies. Many of these trials have reported a clear increase in dystrophin protein follow
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Autor:
Matthew Ellis, J. Malhotra, A. Dugar, Lucy Feng, E. Koenig, Shawn Harriman, D. Scaglioni, F. Catapano, Jennifer E. Morgan, S. Husayni, D. Steiner, S. Torelli, Rahul Phadke, D. Chambers, F. Muntoni
Publikováno v:
Neuromuscular Disorders. 30:S81-S82
Autor:
S. Torelli, Matthew Ellis, Rahul Phadke, A. Sigurta, Lucy Feng, Mervyn Singer, D. Scaglioni, Valentina Sardone, F. Muntoni, Neil E. Hill, Saima Saeed, Caroline Sewry
Publikováno v:
Neuromuscular Disorders. 28:S145-S146
Autor:
Lucy Feng, D. Scaglioni, Pierpaolo Ala, Anna Sarkozy, S. Torelli, D. Ardicli, R. Mein, F. Muntoni, Rahul Phadke, A. Richard-Loendt, Sara Aguti, D. Chambers, M. Beck, Haiyan Zhou, Caroline Sewry
Publikováno v:
Neuromuscular Disorders. 29:S194
Autor:
Jennifer E. Morgan, S. Torelli, Matthew Ellis, D. Scaglioni, Caroline Sewry, Rahul Phadke, Lucy Feng, D. Chambers, F. Muntoni, F. Catapano
Publikováno v:
Neuromuscular Disorders. 29:S90
Autor:
Joana Domingos, Maud Beuvin, Giorgio Tasca, Deborah M. Eastwood, Matthew Ellis, Lucy Feng, D. Scaglioni, F. Leturcq, R. Ben Yaour, Jennifer E. Morgan, F. Muntoni, Gisèle Bonne, Caroline Sewry, Valentina Sardone, Enzo Ricci, S. Torelli, Rahul Phadke, A. Jones
Publikováno v:
Neuromuscular Disorders. 29:S90
Autor:
Valeria Ricotti, L. Phillips, K. Maresh, Andreea Mihaela Seferian, Erik H. Niks, V. Selby, Pierpaolo Ala, Joana Domingos, F. Muntoni, M. van der Holst, D. Scaglioni, Yvonne D. Krom, J.J.G. Verschuuren, V. Straub, L. Servais, F. Catapano, Jennifer E. Morgan, I.J.M. de Groot, T. Voit
Publikováno v:
Neuromuscular Disorders. 29:S90