Zobrazeno 1 - 10 of 16 pro vyhledávání: '"Craig Penz"'
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Akademický článek
Data-driven epidemiologic approach to conducting site feasibility for a global phase III tuberculosis vaccine clinical trial.
Autor: Wai-Ling Mui, Falgunee K Parekh, Ashley S Tseng, Joy Toro, Taylor Craig, Maggwa Ndugga, Alexander C Schmidt, Alemnew F Dagnew, Craig Penz, Ghiorghis Belai
Publikováno v: PLOS Global Public Health, Vol 3, Iss 11, p e0002544 (2023)
An efficacious tuberculosis (TB) vaccine is critical to reducing the global burden of TB. TB vaccine trials require the identification of multiple sites globally that have both a high incidence of TB and the capacity to conduct a clinical trial. To e
Externí odkaz: https://doaj.org/article/ac6205ca11184e8e93720ffbe2dd9a06
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EXPLORE: A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks
Autor: Herbert L. Bonkovsky, D. Montgomery Bissell, Félix Alegre, Amy Simon, Aasne K. Aarsand, Shangbin Liu, Karl E. Anderson, Robert J. Desnick, Michael Norman Badminton, Penelope E. Stein, Neila Talbi, Maria Domenica Cappellini, Amy Chan, Pauline Harper, Elisabeth I. Minder, Manisha Balwani, Janice Andersen, Laurent Gouya, Raili Kauppinen, William Querbes, David C. Rees, Hetanshi Naik, Janneke G. Langendonk, Sverre Sandberg, Aneta Ivanova, John D. Phillips, Tim Lin, John J. Ko, Radan Bruha, Ulrich Stölzel, Eliane Sardh, Jerzy Windyga, Charles J. Parker, Jean Charles Deybach, Craig Penz, Paolo Ventura
Publikováno v: Gouya, L, Ventura, P, Balwani, M, Bissell, D M, Rees, D C, Stölzel, U, Phillips, J D, Kauppinen, R, Langendonk, J G, Desnick, R J, Deybach, J C, Bonkovsky, H L, Parker, C, Naik, H, Badminton, M, Stein, P E, Minder, E, Windyga, J, Bruha, R, Cappellini, M D, Sardh, E, Harper, P, Sandberg, S, Aarsand, A K, Andersen, J, Alegre, F, Ivanova, A, Talbi, N, Chan, A, Querbes, W, Ko, J, Penz, C, Liu, S, Lin, T, Simon, A & Anderson, K E 2019, ' EXPLORE : A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks ', Hepatology . https://doi.org/10.1002/hep.30936
Hepatology, 71(5), 1546-1558. John Wiley & Sons Ltd.
Hepatology (Baltimore, Md.)
Acute hepatic porphyria comprises a group of rare, genetic diseases caused by mutations in genes involved in heme biosynthesis. Patients can experience acute neurovisceral attacks, debilitating chronic symptoms, and long-term complications. There is
Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2b4d56697a99116329133661e8d7e805
http://hdl.handle.net/10138/316254
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Patient Perspective on Acute Intermittent Porphyria with Frequent Attacks: A Disease with Intermittent and Chronic Manifestations
Autor: Jae B. Kim, William Querbes, Amy Simon, Patrick Marquis, Alex Wei, Sonalee Agarwal, Jessica R. Hungate, Desiree Lyon Howe, Farrah Pompilus, Sara Strzok, Craig Penz
Publikováno v: The Patient
Objective Acute intermittent porphyria is a rare metabolic disorder that affects heme synthesis. Patients with acute intermittent porphyria may experience acute debilitating neurovisceral attacks that require frequent hospitalizations and negatively
Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::17839a5936ac428b0716f47f2aa1515c
https://doi.org/10.1007/s40271-018-0319-3
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5
Overall Health, Daily Functioning, and Quality of Life in Acute Hepatic Porphyria Patients: ENVISION, a Phase 3 Global, Multicenter, Randomized, Double-Blind, Placebo-Controlled Trial
Autor: Eliane Sardh, Ulrich Stölzel, Gayle Ross, Daphne Vassiliou, Jerzy Windyga, Charles J. Parker, Amy Simon, Sioban Keel, Raili Kauppinen, Craig Penz, T. Lin, Janneke G. Langendonk, Yutaka Horie, Paolo Ventura, Penelope E. Stein, A. Sasapu, Bruce Ritchie, Bruce Wang, Aneta Ivanova, Laurent Gouya, Peter Stewart, John D. Phillips, Delia D'Avola, T. Nakahara, Manisha Balwani, Karl E. Anderson, D.M. Bissell, David C. Rees, P. Aguilera Peiro, Herbert L. Bonkovsky, Pauline Harper, Samuel M. Silver, Jeeyoung Oh, John J. Ko, Jiaan-Der Wang, O. Hother-Nielsen, M.J. Lee, Sushama Scalera
Publikováno v: Sardh, E, Gouya, L, Rees, D C, Stein, P, Stoelzel, U, Aguilera Peiro, P, Bissell, D M, Bonkovsky, H L, Keel, S, Parker, C, Phillips, J D, Silver, S, Windyga, J, D'Avola, D, Ross, G, Stewart, P, Ritchie, B, Oh, J, Harper, P, Wang, J D, Langendonk, J G, Ivanova, A, Horie, Y, Anderson, K E, Ventura, P, Kauppinen, R, Vassiliou, D, Wang, B, Hother-Nielsen, O, Nakahara, T, Lee, M J, Sasapu, A, Scalera, S, Lin, T, Penz, C, Simon, A, Ko, J & Balwani, M 2020, ' Overall Health, Daily Functioning, and Quality of Life in Acute Hepatic Porphyria Patients : ENVISION, a Phase 3 Global, Multicenter, Randomized, Double-Blind, Placebo-Controlled Trial ', Digestive and Liver Disease, vol. 52, no. Suppl. 1, pp. E35 . https://doi.org/10.1016/j.dld.2019.12.123
Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4a3c86a09a54fd6ef507322b981490dd
https://doi.org/10.1016/j.dld.2019.12.123
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