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pro vyhledávání: '"Collaborative, for the Mucopolysaccharidosis I Intrathecal Research"'
Autor:
Dickson, Patricia I, Kaitila, Ilkka, Harmatz, Paul, Mlikotic, Anton, Chen, Agnes H, Victoroff, Alla, Passage, Merry B, Madden, Jacqueline, Le, Steven Q, Naylor, David E, Collaborative, for the Mucopolysaccharidosis I Intrathecal Research
Publikováno v:
Molecular Genetics and Metabolism, vol 116, iss 1-2
© 2015 Elsevier Inc. Enzyme replacement therapy with laronidase (recombinant human alpha-l-iduronidase) is successfully used to treat patients with mucopolysaccharidosis type I (MPS I). However, the intravenously-administered enzyme is not expected
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=od_______325::bea37cbb113d4637f374e1b894a30845
https://escholarship.org/uc/item/11b4r650
https://escholarship.org/uc/item/11b4r650
