Stress-Induced Mouse Model of the Cardiac Manifestations of Friedreich's Ataxia Corrected by AAV-mediated Gene Therapy.

Autor: Salami CO; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Jackson K; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Jose C; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Alyass L; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Cisse GI; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., De BP; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Stiles KM; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Chiuchiolo MJ; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Sondhi D; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Crystal RG; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA., Kaminsky SM; Department of Genetic Medicine, Weill Cornell Medical College, New York, New York, USA.

Publikováno v: Human gene therapy [Hum Gene Ther] 2020 Aug; Vol. 31 (15-16), pp. 819-827.