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pro vyhledávání: '"Christoph J Niemietz"'
Autor:
Christoph J Niemietz, Vanessa Sauer, Jacqueline Stella, Lutz Fleischhauer, Gursimran Chandhok, Sarah Guttmann, Yesim Avsar, Shuling Guo, Elizabeth J Ackermann, Jared Gollob, Brett P Monia, Andree Zibert, Hartmut H-J Schmidt
Publikováno v:
PLoS ONE, Vol 11, Iss 9, p e0161455 (2016)
Familial amyloid polyneuropathy (FAP) is caused by mutations of the transthyretin (TTR) gene, predominantly expressed in the liver. Two compounds that knockdown TTR, comprising a small interfering RNA (siRNA; ALN-TTR-02) and an antisense oligonucleot
Externí odkaz:
https://doaj.org/article/1796834c54db428483d9067e5e8d8e11