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Tento výsledek nelze pro nepřihlášené uživatele zobrazit.
K zobrazení výsledku je třeba se přihlásit.

Precise therapeutic gene correction by a simple nuclease-induced double-stranded break.

Autor: Iyer S; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, MA, USA., Suresh S; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, MA, USA., Guo D; Department of Neurology, University of Massachusetts Medical School, Worcester, MA, USA.; Wellstone Muscular Dystrophy Program, University of Massachusetts Medical School, Worcester, MA, USA., Daman K; Department of Neurology, University of Massachusetts Medical School, Worcester, MA, USA.; Wellstone Muscular Dystrophy Program, University of Massachusetts Medical School, Worcester, MA, USA., Chen JCJ; Department of Neurology, University of Massachusetts Medical School, Worcester, MA, USA.; Wellstone Muscular Dystrophy Program, University of Massachusetts Medical School, Worcester, MA, USA.; Office of the Vice-Principal (Research), Queen's University, Kingston, Ontario, Canada., Liu P; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, MA, USA., Zieger M; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA.; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA., Luk K; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, MA, USA., Roscoe BP; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, MA, USA.; COGEN Therapeutics, Cambridge, MA, USA., Mueller C; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA.; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA., King OD; Department of Neurology, University of Massachusetts Medical School, Worcester, MA, USA.; Wellstone Muscular Dystrophy Program, University of Massachusetts Medical School, Worcester, MA, USA., Emerson CP Jr; Department of Neurology, University of Massachusetts Medical School, Worcester, MA, USA. charles.emersonjr@umassmed.edu.; Wellstone Muscular Dystrophy Program, University of Massachusetts Medical School, Worcester, MA, USA. charles.emersonjr@umassmed.edu.; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA. charles.emersonjr@umassmed.edu., Wolfe SA; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, MA, USA. scot.wolfe@umassmed.edu.; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA. scot.wolfe@umassmed.edu.; Department of Biochemistry and Molecular Pharmacology, University of Massachusetts Medical School, Worcester, MA, USA. scot.wolfe@umassmed.edu.

Publikováno v: Nature [Nature] 2019 Apr; Vol. 568 (7753), pp. 561-565. Date of Electronic Publication: 2019 Apr 03.