Zobrazeno 1 - 10
of 31
pro vyhledávání: '"Catherine E. Mcguinn"'
Autor:
Mark T Reding, Maria Elisa Mancuso, Suchitra Acharya, Sanjay Ahuja, Maria Teresa Álvarez-Román, Lisa N Boggio, Meera B. Chitlur, Abraham Salvador Majluf-Cruz, Amy L Dunn, Miguel Escobar, Annie Harroche, Maissaa Janbain, Craig M. Kessler, Philip Maes, Catherine E. McGuinn, Danielle Nance, Ulrike Nowak-Göttl, Robert F. Sidonio, Jr., Duc Q Tran, Michael Wang, Jerzy Windyga, Hongying Wang, Thomas Wilkinson, Steven W. Pipe
Publikováno v:
Blood. 140:5597-5599
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::5165acfa7286ae91311397fcb6aeabb4
https://doi.org/10.1182/blood-2022-156110
https://doi.org/10.1182/blood-2022-156110
Publikováno v:
Haemophilia. 28:523-531
Hereditary factor X (FX) deficiency (FXD) is a rare autosomal recessive bleeding disorder. Plasma-derived FX (pdFX) is a high-purity FX concentrate approved in the United States and Europe for the treatment and prophylaxis of bleeding episodes and fo
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::50f222d58f674d48a12c2b0cfc80d3b9
https://doi.org/10.1111/hae.14570
https://doi.org/10.1111/hae.14570
Autor:
R. Liesner, Erik Berntorp, Sharyne Donfield, Amy D. Shapiro, Munira Borhany, Stacy E. Croteau, Susan Kearney, Cristina Tarango, Christoph Bidlingmaier, Catherine E. McGuinn, Yasmina L. Abajas, Manuela Carvalho, Roshni Kulkarni, Jan Astermark, Petra LeBeau, Philip Kuriakose, Christine M. Knoll, Stefan Lethagen, Michelle Witkop, Katharina Holstein, Alice J. Cohen, Margaret V. Ragni, Suchitra S. Acharya, Johannes Oldenburg, Eva Funding, Ulrike M. Reiss, Christine L. Kempton, Michael D. Tarantino
Publikováno v:
Haemophilia. 27:49-59
Haemophilia B (HB) is less well studied than haemophilia A (HA); despite similarities between the two inherited bleeding disorders, important differences remain that require further research.B-Natural is a multi-centre, prospective, observational stu
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e05daff7a3934a8a48410198044c5bcf
https://doi.org/10.1111/hae.14139
https://doi.org/10.1111/hae.14139
Autor:
Amy D. Shapiro, B. Gangadharan, J. Bowen, Christoph Male, Helmut Schweiger, C. J. Hofbauer, Verena Berg, Elena Santagostino, Michael Recht, Margaret V. Ragni, Janice M. Staber, Deborah L Brown, Jenny Klintman, Shannon L. Meeks, Birgit M. Reipert, Karin Fijnvandraat, Hassan M. Yaish, Jan Blatny, Catherine E. McGuinn, Eric S. Mullins, Vlad C. Radulescu
Publikováno v:
Blood Adv
Blood advances, 4(22), 5785-5796. American Society of Hematology
Blood advances, 4(22), 5785-5796. American Society of Hematology
Preventing factor VIII (FVIII) inhibitors following replacement therapies with FVIII products in patients with hemophilia A remains an unmet medical need. Better understanding of the early events of evolving FVIII inhibitors is essential for risk ide
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::681fd965767be44a9de0a71548b5d13f
https://doi.org/10.1182/bloodadvances.2020002731
https://doi.org/10.1182/bloodadvances.2020002731
Autor:
Karen L. Zimowski, Glaivy Batsuli, Corinna L. Schultz, Catherine E. McGuinn, Shipra Kaicker, Yasmina L. Abajas
Publikováno v:
Journal of Thrombosis and Haemostasis. 18:2551-2556
BACKGROUND Congenital factor X deficiency (FXD) is a rare bleeding disorder that often presents with severe bleeding in the neonatal period. Long-term prophylaxis with infusions of FX-containing products is recommended in patients with FXD and a pers
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4fdf5caefe1c1d483ef7444a32879d93
https://doi.org/10.1111/jth.14985
https://doi.org/10.1111/jth.14985
Autor:
Catherine E. McGuinn, Hannah Fassel
Publikováno v:
Br J Haematol
Haemophilia is an inherited bleeding disorder in which the haemostatic defect results from deficiency of coagulation factor VIII (FVIII) in haemophilia A or factor IX (FIX) in haemophilia B. Traditional treatments for haemophilia have largely worked
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::13b3f0c69d5fc7cc303cd908a14d4165
https://pubmed.ncbi.nlm.nih.gov/34340257
https://pubmed.ncbi.nlm.nih.gov/34340257
Autor:
Katie Bergstrom, Yigal Dror, Kathleen Overholt, Melissa J. Rose, Paul Castillo, Beth A Carella, Kristin A. Shimano, Bonnie W Lau, James N. Huang, Larisa Broglie, Evan Shereck, Steven W. Allen, Timothy S. Olson, Jessica Boklan, Anupama Narla, Catherine E. McGuinn, Taizo A. Nakano, Adrianna Vlachos, Marcin W. Wlodarski, Amy E. Geddis, Nicholas J. Gloude, Jill L. O. de Jong, Anjali Sharathkumar, Jennifer A. Rothman, Akiko Shimamura, Alison A. Bertuch
Publikováno v:
American journal of hematologyREFERENCES. 96(11)
The North American Pediatric Aplastic Anemia Consortium (NAPAAC) is a group of pediatric hematologist-oncologists, hematopathologists, and bone marrow transplant physicians from 46 institutions in North America with interest and expertise in aplastic
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::11dc98ef0351af66663ab855bc7c1e77
https://pubmed.ncbi.nlm.nih.gov/34342889
https://pubmed.ncbi.nlm.nih.gov/34342889
Autor:
Jonathan M. Ducore, John E.J. Rasko, Lynne Smith, Adam Giermasz, Jerome M. Teitel, A Chhabra, Spencer K. Sullivan, Jeremy Rupon, Ben J. Samelson-Jones, Lindsey A. George, Amanda C. O’Brien, Catherine E. McGuinn, Ian Winburn
Publikováno v:
Blood. 138:3975-3975
Fifteen patients with moderately severe to severe hemophilia B (factor IX [FIX] activity ≤2%) were treated with fidanacogene elaparvovec at a dose of 5e11 vg/kg as part of a phase 1/2a study. The study was 52 weeks in duration, after which patients
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::52b8ffb486f165d405e74851019539ff
https://doi.org/10.1182/blood-2021-150541
https://doi.org/10.1182/blood-2021-150541
Autor:
Joanna A. Davis, Allison P. Wheeler, J. Sanders, Shannon L. Carpenter, Ming Y. Lim, James French, Steven W. Pipe, Amit Soni, Michael D. Tarantino, Dunlei Cheng, Amy D. Shapiro, C. Knoll, Ralph A. Gruppo, Catherine E. McGuinn, Amy L. Dunn, Sanjay P Ahuja, Robert F. Sidonio, Dagmar Stein, Ruchika Sharma, Diane J. Aschman, Guy Young
Publikováno v:
Haemophilia. 23:e385-e388
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::549428f2f5a4a2a1c0ab0d8901195276
https://doi.org/10.1111/hae.13273
https://doi.org/10.1111/hae.13273
Autor:
Steven W. Pipe, Christine M. Knoll, Roshni Kulkarni, Suchitra S. Acharya, Craig D. Seaman, Marnie Bertolet, Deborah Vehec, Ulrike M. Reiss, Shannon L. Carpenter, Amy L. Dunn, Courtney D. Thornburg, Nina Hwang, Rosa E. Diaz, Maria M. Brooks, Allison P. Wheeler, Guy Young, Frederico Xavier, Cindy A. Leissinger, Margaret V. Ragni, Maria Velez, Vilmarie Rodriguez, Lynn M. Malec, Catherine E. McGuinn, Dana Ivanco, Eric J. Werner, Shelley E. Crary, Erin Cockrell, Cristina Tarango, Tamara Haller, Courtney E. Lawrence, Irmel Ayala, Tiffany Lin Lucas, Michael Wang, Sanjay P Ahuja, Joseph L Lasky, Deborah L Brown, Meera Chitlur
Publikováno v:
Blood. 136:14-15
Introduction: Among the most challenging complications of hemophilia A is inhibitor formation. A T-cell dependent B-cell response to exogenous factor VIII (FVIII), inhibitors result in a high burden of disease, with poorly controlled bleeding, twice
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::89db6225a518eeb0eebcf160f3225da4
https://doi.org/10.1182/blood-2020-136814
https://doi.org/10.1182/blood-2020-136814