The use or generation of biomedical data and existing medicines to discover and establish new treatments for patients with rare diseases – recommendations of the IRDiRC Data Mining and Repurposing Task Force

Autor: Noel T Southall, Madhusudan Natarajan, Lilian Pek Lian Lau, Anneliene Hechtelt Jonker, Benoît Deprez, Tim Guilliams, Lawrence Hunter, Carin MA Rademaker, Virginie Hivert, Diego Ardigò, on behalf of the IRDiRC Data Mining and Repurposing Task Force

Publikováno v: Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-8 (2019)

Abstract The number of available therapies for rare diseases remains low, as fewer than 6% of rare diseases have an approved treatment option. The International Rare Diseases Research Consortium (IRDiRC) set up the multi-stakeholder Data Mining and R

Externí odkaz: https://doaj.org/article/35fa88c515684ce8ae77763bca186370

Solid Oral Flexible Formulations for Paediatric and Geriatric patients: Age-appropriate Formulation Platforms.

Autor: CHANDRASEKARAN, P.¹, KANDASAMY, RUCKMANI¹ hodpharma@gmail.com

Publikováno v: Indian Journal of Pharmaceutical Sciences. Jan/Feb2018, Vol. 80 Issue 1, p14-25. 12p.

The use or generation of biomedical data and existing medicines to discover and establish new treatments for patients with rare diseases - recommendations of the IRDiRC Data Mining and Repurposing Task Force.

Autor: Southall, Noel T¹ (AUTHOR) southalln@mail.nih.gov, Natarajan, Madhusudan² (AUTHOR), Lau, Lilian Pek Lian^1,3 (AUTHOR), Jonker, Anneliene Hechtelt³ (AUTHOR), Deprez, Benoît^4,5 (AUTHOR), Guilliams, Tim⁶ (AUTHOR), Hunter, Lawrence⁷ (AUTHOR), Rademaker, Carin MA⁸ (AUTHOR), Hivert, Virginie⁹ (AUTHOR), Ardigò, Diego¹⁰ (AUTHOR), on behalf of the IRDiRC Data Mining and Repurposing Task Force (AUTHOR), Cavalla, David (AUTHOR), Colvis, Christine (AUTHOR), Hettne, Kristina (AUTHOR), 't-Hoen, Peter-Bram (AUTHOR), Kant, Caroline (AUTHOR), Krischer, Jeffrey (AUTHOR), Marin, Frédéric (AUTHOR), Quintana, Jordi (AUTHOR), Rademaker, Carin MA (AUTHOR)

Publikováno v: Orphanet Journal of Rare Diseases. 10/15/2019, Vol. 14 Issue 1, pN.PAG-N.PAG. 1p.