Zobrazeno 1 - 10
of 134
pro vyhledávání: '"Bernhard, Gentner"'
Autor:
Daniela Cesana, Maria Pia Cicalese, Andrea Calabria, Pietro Merli, Roberta Caruso, Monica Volpin, Laura Rudilosso, Maddalena Migliavacca, Federica Barzaghi, Claudia Fossati, Francesco Gazzo, Simone Pizzi, Andrea Ciolfi, Alessandro Bruselles, Francesca Tucci, Giulio Spinozzi, Giulia Pais, Fabrizio Benedicenti, Matteo Barcella, Ivan Merelli, Pierangela Gallina, Stefania Giannelli, Francesca Dionisio, Serena Scala, Miriam Casiraghi, Luisa Strocchio, Luciana Vinti, Lucia Pacillo, Eleonora Draghi, Marcella Cesana, Sara Riccardo, Chiara Colantuono, Emmanuelle Six, Marina Cavazzana, Filippo Carlucci, Manfred Schmidt, Caterina Cancrini, Fabio Ciceri, Luca Vago, Davide Cacchiarelli, Bernhard Gentner, Luigi Naldini, Marco Tartaglia, Eugenio Montini, Franco Locatelli, Alessandro Aiuti
Publikováno v:
Nature Communications, Vol 15, Iss 1, Pp 1-18 (2024)
Abstract Hematopoietic stem cell gene therapy (GT) using a γ-retroviral vector (γ-RV) is an effective treatment for Severe Combined Immunodeficiency due to Adenosine Deaminase deficiency. Here, we describe a case of GT-related T-cell acute lymphobl
Externí odkaz:
https://doaj.org/article/319bd86d084c40b6be16ee73e0b5af1a
Autor:
Fabio Ciceri, Alessandro Olivi, Valeria Ferla, PAOLO FERROLI, Francesca Farina, Carlo Russo, Bernhard Gentner, Marica Eoli, Elena Anghileri, Matteo Barcella, Valentina Brambilla, Matteo Carrabba, Valeria Cuccarini, Giorgio D’Alessandris, Francesco Di Meco, Filippo Gagliardi, Federico Legnani, Stefania Mazzoleni, Roberto Pallini, Marco Saini, Silvia Snider, Karen Mullen, Luigi Naldini, Gaetano Finocchiaro
Publikováno v:
Journal for ImmunoTherapy of Cancer, Vol 11, Iss Suppl 1 (2023)
Externí odkaz:
https://doaj.org/article/a228f1de6a04426aabea4c7d530a3ccc
Autor:
Daniela Magliulo, Matilde Simoni, Carolina Caserta, Cristina Fracassi, Serena Belluschi, Kety Giannetti, Raffaella Pini, Ettore Zapparoli, Stefano Beretta, Martina Uggè, Eleonora Draghi, Federico Rossari, Nadia Coltella, Cristina Tresoldi, Marco J Morelli, Raffaella Di Micco, Bernhard Gentner, Luca Vago, Rosa Bernardi
Publikováno v:
EMBO Molecular Medicine, Vol 15, Iss 11, Pp n/a-n/a (2023)
Abstract One of the defining features of acute myeloid leukemia (AML) is an arrest of myeloid differentiation whose molecular determinants are still poorly defined. Pharmacological removal of the differentiation block contributes to the cure of acute
Externí odkaz:
https://doaj.org/article/2d1702404ed248f580d807aa7c1fabee
Autor:
Matteo Maria Naldini, Gabriele Casirati, Matteo Barcella, Paola Maria Vittoria Rancoita, Andrea Cosentino, Carolina Caserta, Francesca Pavesi, Erika Zonari, Giacomo Desantis, Diego Gilioli, Matteo Giovanni Carrabba, Luca Vago, Massimo Bernardi, Raffaella Di Micco, Clelia Di Serio, Ivan Merelli, Monica Volpin, Eugenio Montini, Fabio Ciceri, Bernhard Gentner
Publikováno v:
Nature Communications, Vol 14, Iss 1, Pp 1-20 (2023)
Relapse within acute myeloid leukaemia may be driven by the presence of leukaemia stem cells. Here, the authors use single cell RNA-seq seq to characterise leukemia stem cells, and show miR-126 as a potential marker of resistance.
Externí odkaz:
https://doaj.org/article/e9cf4c7e50174415ac6b0136a26fcea7
Autor:
Pamela Quaranta, Luca Basso-Ricci, Raisa Jofra Hernandez, Matteo Maria Naldini, Matteo Barcella, Guido Pacini, Carlo Pietrasanta, Lorenza Pugni, Giulia Pais, Fabrizio Benedicenti, Stefania Giannelli, Ilaria Monti, Silvia Darin, Graziano Barera, Francesca Tucci, Francesca Ferrua, Valeria Calbi, Bernhard Gentner, Raffaella DI Micco, Eugenio Montini, Andrea Calabria, Ivan Merelli, Fabio Mosca, Maria Ester Bernardo, Maria Pia Cicalese, Alessandro Aiuti, Scala Serena
Publikováno v:
HemaSphere, Vol 7, p e78878d6 (2023)
Externí odkaz:
https://doaj.org/article/5db5ca39edba4d99b8ab8a0bef415a24
Autor:
Pier Edoardo Rovatti, Marco Punta, Matteo Maria Naldini, Matteo Barcella, Laura Zito, Matteo Giovanni Carrabba, Massimo Bernardi, Jacopo Peccatori, Ivan Merelli, Bernhard Gentner, Fabio Ciceri, Luca Vago, Cristina Toffalori
Publikováno v:
HemaSphere, Vol 7, p e908160d (2023)
Externí odkaz:
https://doaj.org/article/e87adfa2d3ba42719a1fd7dcb0505a22
Autor:
Martina Fiumara, Samuele Ferrari, Attya Omer-Javed, Stefano Beretta, Luisa Albano, Daniele Canarutto, Angelica Varesi, Chiara Gaddoni, Chiara Brombin, Federica Cugnata, Erika Zonari, Matteo Maria Naldini, Matteo Barcella, Bernhard Gentner, Ivan Merelli, Luigi Naldini
Publikováno v:
HemaSphere, Vol 7, p e6237653 (2023)
Externí odkaz:
https://doaj.org/article/4dacf51b000c4c6baa7cbba5fcb5b5e7
Autor:
Francesca Tucci, Giulia Consiglieri, Chiara Filisetti, Maurizio De Pellegrin, Renata Mellone, Francesca Fumagalli, Silvia Darin, Marina Sarzana, Stefano Scarparo, Francesca Ciotti, Paolo Silvani, Cristina Baldoli, Silvia Pontesilli, Rossella Parini, Giancarlo la Marca, Fabio Ciceri, Luigi Naldini, Alessandro Aiuti, Bernhard Gentner, Maria Ester Bernardo
Publikováno v:
HemaSphere, Vol 7, p e1995859 (2023)
Externí odkaz:
https://doaj.org/article/5cc196069a7d4d9f9d64fc9f8b434e34
Autor:
Daniele Canarutto, Francesca Tucci, Salvatore Gattillo, Matilde Zambelli, Valeria Calbi, Bernhard Gentner, Francesca Ferrua, Sarah Marktel, Maddalena Migliavacca, Federica Barzaghi, Giulia Consiglieri, Vera Gallo, Francesca Fumagalli, Paola Massariello, Cristina Parisi, Gianluca Viarengo, Elena Albertazzi, Paolo Silvani, Raffaella Milani, Luca Santoleri, Fabio Ciceri, Maria Pia Cicalese, Maria Ester Bernardo, Alessandro Aiuti
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 22, Iss , Pp 76-83 (2021)
Hematopoietic stem and progenitor cell (HSPC)-based gene therapy (GT) requires the collection of a large number of cells. While bone marrow (BM) is the most common source of HSPCs in pediatric donors, the collection of autologous peripheral blood ste
Externí odkaz:
https://doaj.org/article/78fa1749ad2c4919b4ea903983d1ea2f
Autor:
Luigi Naldini, Maria Pia Cicalese, Maria Ester Bernardo, Bernhard Gentner, Michela Gabaldo, Giuliana Ferrari, Alessandro Aiuti
Publikováno v:
HemaSphere, Vol 6, Iss 2, p e671 (2022)
Externí odkaz:
https://doaj.org/article/f0a3af6429944f7aaabff2c58a1b2e5f