Zobrazeno 1 - 10
of 99
pro vyhledávání: '"Banik, Rudrani"'
Autor:
Yu-Wai-Man, Patrick, Carelli, Valerio, Newman, Nancy J., Silva, Magda Joana, Linden, Aki, Van Stavern, Gregory, Szaflik, Jacek P., Banik, Rudrani, Lubiński, Wojciech, Pemp, Berthold, Liao, Yaping Joyce, Subramanian, Prem S., Misiuk-Hojło, Marta, Newman, Steven, Castillo, Lorena, Kocięcki, Jarosław, Levin, Marc H., Muñoz-Negrete, Francisco Jose, Yagan, Ali, Cherninkova, Sylvia, Katz, David, Meunier, Audrey, Votruba, Marcela, Korwin, Magdalena, Dziedziak, Jacek, Jurkutė, Neringa, Harvey, Joshua P., La Morgia, Chiara, Priglinger, Claudia, Llòria, Xavier, Tomasso, Livia, Klopstock, Thomas
Publikováno v:
In Cell Reports Medicine 19 March 2024 5(3)
Autor:
VIGNAL-CLERMONT, CATHERINE, YU-WAI-MAN, PATRICK, NEWMAN, NANCY J., CARELLI, VALERIO, MOSTER, MARK L., BIOUSSE, VALERIE, SUBRAMANIAN, PREM S., WANG, AN-GUOR, DONAHUE, SEAN P., LEROY, BART P., SADUN, ALFREDO A., KLOPSTOCK, THOMAS, SERGOTT, ROBERT C., REBOLLEDA FERNANDEZ, GEMA, CHWALISZ, BART K., BANIK, RUDRANI, TAIEL, MAGALI, ROUX, MICHEL, SAHEL, JOSÉ-ALAIN
Publikováno v:
In American Journal of Ophthalmology May 2023 249:108-125
Autor:
Nancy J Newman, Valérie Biousse, José-Alain Sahel, Patrick Yu-Wai-Man, Sean Donahue, Gema Rebolleda, Prem S Subramanian, Bart P Leroy, Alfredo A Sadun, Robert C Sergott, Catherine Vignal-Clermont, Bart K Chwalisz, Mark Moster, An-Guor Wang, Valerio Carelli, Rudrani Banik, Fabienne Bazin, Eric Cox, Michel Roux, Magali Taiel, Amore Giulia, Anand Shweta, Banik Rudrani, Barboni Piero, Biousse Valérie, Boston Hayley, Burale Asma, Carbonelli Michele, Carelli Valerio, Chen Celia, Cheng Hui-Chen, Cho Steve, K Chwalisz Bart, Contin Manuela, D’Agati Pietro, A DeBusk Adam, De Zaeytijd Julie, Dobbs Jannah, P Donahue Sean, DuBois Lindreth, Esposti Simona, Fernandes Filho Alcides, Fortin Elizabeth, Gangaputra Sapna, Gibbs Deborah, Girmens Jean François, Hage Rabih, A Haller Julia, Heilweil Gad, Hubbard III GeorgeBaker, Hwang Jeong-Min, Jaumendreu Urquijo Laia, Jurkute Neringa, Karanjia Rustum, Khemliche Wahiba, La Morgia Chiara, P Leroy Bart, Massini Maria, Mathias Marc, A Memon Muhammad, Mohamed Susan, L Moster Mark, J Muñoz NegreteFrancisco, J Newman Nancy, O’Keefe Ghazala, Patel Shriji, Pecen Paula, H Peragallo Jason, Plaine Lise, Preston Mary, Rebolleda Fernández Gema, Romagnoli Martina, A Sadun Alfredo, A Sahel José, SantaMaria Melissa, C Sergott Robert, S Subramanian Prem, Sun Chuanbin, Tai Katy, Tollis Heather, Tsui Irena, R Tucker William, Vignal-Clermont Catherine, Wang An-Guor, Wilkins Saige, Yu-Wai-Man Patrick
Publikováno v:
BMJ Open Ophthalmology, Vol 7, Iss 1 (2022)
Objective REFLECT is the first randomised, double-masked, placebo-controlled multicentre phase 3 clinical trial that evaluated the efficacy and safety of bilateral intravitreal (IVT) injection of lenadogene nolparvovec in subjects with Leber heredita
Externí odkaz:
https://doaj.org/article/c3ae820deb6448238032cfa7c2f4a8d2
Autor:
Loewenstern, Joshua, Hernandez, Christopher M., Chadwick, Carolyn, Doshi, Amish, Banik, Rudrani, Sarkiss, Christopher A., Bederson, Joshua, Shrivastava, Raj K.
Publikováno v:
In World Neurosurgery January 2018 109:e546-e553
Akademický článek
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Autor:
Newman, Nancy J, Yu-Wai-Man, Patrick, Subramanian, Prem S, Moster, Mark L, Wang, An-Guor, Donahue, Sean P, Leroy, Bart P, Carelli, Valerio, Biousse, Valerie, Vignal-Clermont, Catherine, Sergott, Robert C, Sadun, Alfredo A, Rebolleda Fernández, Gema, Chwalisz, Bart K, Banik, Rudrani, Bazin, Fabienne, Roux, Michel, Cox, Eric D, Taiel, Magali, Sahel, José-Alain, LHON REFLECT Study Group
Publikováno v:
Brain : a journal of neurology, vol 146, iss 4
Leber hereditary optic neuropathy (LHON) is an important example of mitochondrial blindness with the m.11778G>A mutation in the MT-ND4 gene being the most common disease-causing mtDNA variant worldwide. The REFLECT phase 3 pivotal study is a randomiz
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=od_______325::fbc6c14d483c8284335217866cd64e5c
https://escholarship.org/uc/item/7m28c7n9
https://escholarship.org/uc/item/7m28c7n9
Autor:
Vignal-ClermoḤ, Catherine, Yu-Wai-Man, Patrick, Sadun, Alfredo A, Klopstock, Thomas, Sergott, Robert C, Fernández, Gema Rebolleda, Chwalisz, Bart K, Banik, Rudrani, Taiel, Magali, Roux, Michel, Sahel, José-Alain, Group, LHON Study, Newman, Nancy J, Carelli, Valerio, Moster, Mark L, Biousse, Valerie, Subramanian, Prem S, Wang, An-Guor, Donahue, Sean P, Leroy, Bart P
Publikováno v:
American journal of ophthalmology 249, 108-125 (2023). doi:10.1016/j.ajo.2022.11.026
Purpose: Evaluate the safety profile of lenadogene nolparvovec (Lumevoq®) in patients with Leber hereditary optic neuropathy. Design: Pooled analysis of safety data from 5 clinical studies. Methods: A total of 189 patients received single unilateral
Autor:
Carelli, Valerio, Newman, Nancy J, Yu-Wai-Man, Patrick, Biousse, Valerie, Moster, Mark L, Subramanian, Prem S, Vignal-Clermont, Catherine, Wang, An-Guor, Donahue, Sean P, Leroy, Bart P, Sergott, Robert C, Klopstock, Thomas, Sadun, Alfredo A, Rebolleda Fernández, Gema, Chwalisz, Bart K, Banik, Rudrani, Girmens, Jean François, La Morgia, Chiara, DeBusk, Adam A, Jurkute, Neringa, Priglinger, Claudia, Karanjia, Rustum, Josse, Constant, Salzmann, Julie, Montestruc, François, Roux, Michel, Taiel, Magali, Sahel, José-Alain, Group, The LHON Study
Funder: GenSight Biologics
Funder: patients’ organizations MITOCON and IFOND, and patients’ donations
Funder: Fight for Sight UK; doi: http://dx.doi.org/10.13039/501100000615
Funder: Isaac Newton Trust; doi: http://dx.doi.org/10.13
Funder: patients’ organizations MITOCON and IFOND, and patients’ donations
Funder: Fight for Sight UK; doi: http://dx.doi.org/10.13039/501100000615
Funder: Isaac Newton Trust; doi: http://dx.doi.org/10.13
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::a24ae51558b5bef5a137f78c2fbcc7fb
Autor:
Newman, Nancy J., Yu-Wai-Man, Patrick, Subramanian, Prem S., Moster, Mark L., Wang, An-Guor, Donahue, Sean P., Leroy, Bart, Carelli, Valerio, Biousse, Valerie, Vignal-Clermont, Catherine, Sergott, Robert C., Sadun, Alfredo A., Fernandez, Gema Rebolleda, Chwalisz, Bart K., Banik, Rudrani, Bazin, Fabienne, Roux, Michel, Cox, Eric D., Taiel, Magali, Sahel, Jose-Alain, Study Grp, LHON REFLECT
Publikováno v:
BRAIN
Leber hereditary optic neuropathy (LHON) is an important example of mitochondrial blindness with the m.11778G>A mutation in the MT-ND4 gene being the most common disease-causing mtDNA variant worldwide. The REFLECT phase 3 pivotal study is a randomiz
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3b053b101295a09206a957a2d7a7249e
https://biblio.ugent.be/publication/01H2APQR5ZC0W1HHXGJ08XZKEC
https://biblio.ugent.be/publication/01H2APQR5ZC0W1HHXGJ08XZKEC
Akademický článek
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