Zobrazeno 1 - 6
of 6
pro vyhledávání: '"Béatrice Marolleau"'
Autor:
Jean-Baptiste Dupont, Benoit Tournaire, Christophe Georger, Béatrice Marolleau, Laurence Jeanson-Leh, Mireille Ledevin, Pierre Lindenbaum, Emilie Lecomte, Benjamin Cogné, Laurence Dubreil, Thibaut Larcher, Bernard Gjata, Laetitia Van Wittenberghe, Caroline Le Guiner, Magalie Penaud-Budloo, Richard O Snyder, Philippe Moullier, Adrien Léger
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 2, Iss , Pp - (2015)
Preclinical gene therapy strategies using recombinant adeno-associated virus (AAV) vectors in animal models of Duchenne muscular dystrophy have shown dramatic phenotype improvements, but long-lasting efficacy remains questionable. It is believed that
Externí odkaz:
https://doaj.org/article/846a902b7ddb4553bb393762ce9f0d6f
Autor:
Adeline Miranda, Dan Lupo, Federico Mingozzi, Xavier M. Anguela, Joseph Silverberg, Karen Huang, Heena Beck, Saghana Muraleetharan, Béatrice Marolleau, Fanny Collaud, Laetitia van Wittengerghe, Sean M. Armour, Christian Leborgne, Elena Barbon, Sandrine Delignat, Jeffrey M. Alexander, Hayley Hanby, Victoria Daventure, Giuseppe Ronzitti, Sébastien Lacroix-Desmazes, Anna Fabiano, Daniel M. Cohen
Publikováno v:
Nature Medicine
Nature Medicine, Nature Publishing Group, 2020, 26 (7), pp.1096-1101. ⟨10.1038/s41591-020-0911-7⟩
Nature Medicine, 2020, 26 (7), pp.1096-1101. ⟨10.1038/s41591-020-0911-7⟩
Nature Medicine, Nature Publishing Group, 2020, 26 (7), pp.1096-1101. ⟨10.1038/s41591-020-0911-7⟩
Nature Medicine, 2020, 26 (7), pp.1096-1101. ⟨10.1038/s41591-020-0911-7⟩
Neutralizing antibodies to adeno-associated virus (AAV) vectors are highly prevalent in humans1,2, and block liver transduction3–5 and vector readministration6; thus, they represent a major limitation to in vivo gene therapy. Strategies aimed at ov
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ff04724b6af379a7e9370adc25a9aa43
https://hal.archives-ouvertes.fr/hal-03031762
https://hal.archives-ouvertes.fr/hal-03031762
Autor:
Adrien Leger, Bernard Gjata, Benjamin Cogné, Laetitia van Wittenberghe, Benoît Tournaire, Jean-Baptiste Dupont, Alban Vignaud, Christophe Georger, Romain Durand, Béatrice Marolleau, Richard O. Snyder, Emilie Bertil, Emilie Lecomte, Philippe Moullier
Publikováno v:
Les Cahiers de Myologie. :99-101
Autor:
Christian Leborgne, Béatrice Marolleau, Alain Brisson, Casey A. Maguire, Federico Mingozzi, Fabienne Jouen, Laetitia van Wittenberghe, Alban Vignaud, Florence Boisgerault, Olivier D. Christophe, Fanny Collaud, Solenne Marmier, Giuseppe Ronzitti, Olivier Boyer, Zachary Fitzpatrick, Sisareuth Tan, Amine Meliani, Marcelo Simon Sola, Severine Charles
Publikováno v:
Blood Advances
Blood Advances, The American Society of Hematology, 2017, 1 (23), pp.2019-2031. ⟨10.1182/bloodadvances.2017010181⟩
Blood Advances, 2017, 1 (23), pp.2019-2031. ⟨10.1182/bloodadvances.2017010181⟩
Blood Advances, The American Society of Hematology, 2017, 1 (23), pp.2019-2031. ⟨10.1182/bloodadvances.2017010181⟩
Blood Advances, 2017, 1 (23), pp.2019-2031. ⟨10.1182/bloodadvances.2017010181⟩
Results from clinical trials of liver gene transfer for hemophilia demonstrate the potential of the adeno-associated virus (AAV) vector platform. However, to achieve therapeutic transgene expression, in some cases high vector doses are required, whic
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2526ac2de33b1e6b5de9af723d344245
https://hal.archives-ouvertes.fr/hal-02377508
https://hal.archives-ouvertes.fr/hal-02377508
Autor:
Bernard Gjata, Benoît Tournaire, Alban Vignaud, Christophe Georger, Philippe Moullier, Romain Durand, Adrien Leger, Jean-Baptiste Dupont, Emilie Lecomte, Benjamin Cogné, Richard O. Snyder, Emilie Bertil, Béatrice Marolleau, Laetitia vanWittenberghe
Publikováno v:
Molecular Therapy. 24:S155
Recombinant adeno-associated virus (rAAV)-based vectors are promising tools for the treatment of Duchenne muscular dystrophy (DMD) by gene therapy. Following rAAV injection in murine and canine models of DMD, several groups have reported significant
Autor:
Amine Meliani, Florence Boisgerault, Zachary Fitzpatrick, Solenne Marmier, Christian Leborgne, Fanny Collaud, Marcelo Simon Sola, Severine Charles, Giuseppe Ronzitti, Alban Vignaud, Laetitia van Wittenberghe, Beatrice Marolleau, Fabienne Jouen, Sisareuth Tan, Olivier Boyer, Olivier Christophe, Alain R. Brisson, Casey A. Maguire, Federico Mingozzi
Publikováno v:
Blood Advances, Vol 1, Iss 23, Pp 2019-2031 (2017)
Abstract: Results from clinical trials of liver gene transfer for hemophilia demonstrate the potential of the adeno-associated virus (AAV) vector platform. However, to achieve therapeutic transgene expression, in some cases high vector doses are requ
Externí odkaz:
https://doaj.org/article/302c51191d2d4ae38857d80e959d437b