Zobrazeno 1 - 3
of 3
pro vyhledávání: '"Anna Creismeas"'
Autor:
Anna Creisméas, Claire Gazaille, Audrey Bourdon, Marc-Antoine Lallemand, Virginie François, Marine Allais, Mireille Ledevin, Thibaut Larcher, Gilles Toumaniantz, Aude Lafoux, Corinne Huchet, Ignacio Anegon, Oumeya Adjali, Caroline Le Guiner, Bodvaël Fraysse
Publikováno v:
Journal of Translational Medicine, Vol 19, Iss 1, Pp 1-17 (2021)
Abstract Background Duchenne muscular dystrophy (DMD) is an X-linked inherited disease caused by mutations in the gene encoding dystrophin that leads to a severe and ultimately life limiting muscle-wasting condition. Recombinant adeno-associated vect
Externí odkaz:
https://doaj.org/article/df4837365a234a57b360f01bc60d2a4d
Autor:
Audrey Bourdon, Virginie François, Liwen Zhang, Aude Lafoux, Bodvael Fraysse, Gilles Toumaniantz, Thibaut Larcher, Tiphaine Girard, Mireille Ledevin, Cyrielle Lebreton, Agnès Hivonnait, Anna Creismeas, Marine Allais, Basile Marie, Justine Guguin, Véronique Blouin, Séverine Remy, Ignacio Anegon, Corinne Huchet, Alberto Malerba, Betty Kao, Anita Le Heron, Philippe Moullier, George Dickson, Linda Popplewell, Oumeya Adjali, Federica Montanaro, Caroline Le Guiner
Publikováno v:
Gene Therapy. 29:520-535
Autor:
Audrey, Bourdon, Virginie, François, Liwen, Zhang, Aude, Lafoux, Bodvael, Fraysse, Gilles, Toumaniantz, Thibaut, Larcher, Tiphaine, Girard, Mireille, Ledevin, Cyrielle, Lebreton, Agnès, Hivonnait, Anna, Creismeas, Marine, Allais, Basile, Marie, Justine, Guguin, Véronique, Blouin, Séverine, Remy, Ignacio, Anegon, Corinne, Huchet, Alberto, Malerba, Betty, Kao, Anita, Le Heron, Philippe, Moullier, George, Dickson, Linda, Popplewell, Oumeya, Adjali, Federica, Montanaro, Caroline, Le Guiner
Publikováno v:
Gene therapy. 29(9)
Duchenne muscular dystrophy (DMD) is a muscle wasting disorder caused by mutations in the gene encoding dystrophin. Gene therapy using micro-dystrophin (MD) transgenes and recombinant adeno-associated virus (rAAV) vectors hold great promise. To overc