Zobrazeno 1 - 10
of 23
pro vyhledávání: '"Amy Strong"'
Autor:
Ryan S. Paquin, Ryan Fischer, Carol Mansfield, Brennan Mange, Katherine Beaverson, Annie Ganot, Amy Strong Martin, Carl Morris, Colin Rensch, Valeria Ricotti, Leo J. Russo, Alesia Sadosky, Edward C. Smith, Holly L. Peay
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-9 (2019)
Abstract Purpose Several gene therapy trials for Duchenne muscular dystrophy initiated in 2018. Trial decision making is complicated by non-curative, time-limited benefits; the progressive, fatal course; and high unmet needs. Here, caregivers and pat
Externí odkaz:
https://doaj.org/article/9a341e5765cf4d0c818fe5d13af95442
Autor:
Holly L. Peay, Ryan Fischer, Brennan Mange, Ryan S. Paquin, Edward C. Smith, Alesia Sadosky, Leo Russo, Valeria Ricotti, Colin Rensch, Carl Morris, Amy Strong Martin, Annie Ganot, Katherine Beaverson, Carol Mansfield
Publikováno v:
Molecular Genetics & Genomic Medicine, Vol 9, Iss 5, Pp n/a-n/a (2021)
Abstract Background Gene therapy offers an etiologically targeted treatment for genetic disorders. Little is known about the acceptance of mortality risk among patients with progressive, fatal conditions. We assessed patients’ and caregivers’ max
Externí odkaz:
https://doaj.org/article/52d96db984d645b4b1d2e956eedbd260
Autor:
Holly Landrum Peay, Ryan Fischer, Janice P Tzeng, Sharon E Hesterlee, Carl Morris, Amy Strong Martin, Colin Rensch, Edward Smith, Valeria Ricotti, Katherine Beaverson, Hannah Wand, Carol Mansfield
Publikováno v:
PLoS ONE, Vol 14, Iss 5, p e0213649 (2019)
ObjectivesDuchenne muscular dystrophy (DMD) is a rare neuromuscular disorder that causes progressive weakness and early death. Gene therapy is an area of new therapeutic development. This qualitative study explored factors influencing parents' and ad
Externí odkaz:
https://doaj.org/article/dc50ddcfc3d940448acd1b9d4749a014
Publikováno v:
Bio-Protocol, Vol 7, Iss 5 (2017)
Adipose-derived stromal/stem cells (ASCs) are multipotent cells that can be isolated from adipose tissue. Studies have shown that cells have the capacity to self-renew and differentiate into adipocyte, chondrocyte, myocyte, and osteoblast lineages. T
Externí odkaz:
https://doaj.org/article/ff2a0ddfd96f495b9f17df8900ecd46b
Publikováno v:
American Journal of Medical Genetics Part A. 188:3312-3317
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::c227ce7e40750a0828e5419941a13572
https://doi.org/10.1002/ajmg.a.62956
https://doi.org/10.1002/ajmg.a.62956
Publikováno v:
Journal of Medical Robotics Research.
For the safe and effective development of evolving autonomous medical robotic systems that traverse the surface of the body, like in breast ultrasound scans, developing phantoms that are durable and mechanically mimic human tissue is critical. In thi
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::97f8eea23ff4c7f239a0311810f1d597
https://doi.org/10.1142/s2424905x22410100
https://doi.org/10.1142/s2424905x22410100
Autor:
Valeria Ricotti, Holly L. Peay, Amy Strong Martin, Ryan Fischer, Carol Mansfield, Brennan Mange, Colin Rensch, Annie Ganot, Katherine Beaverson, Edward C. Smith, Alesia Sadosky, Ryan S. Paquin, Leo Russo, Carl Morris
Publikováno v:
Molecular Genetics & Genomic Medicine, Vol 9, Iss 5, Pp n/a-n/a (2021)
Molecular Genetics & Genomic Medicine
Molecular Genetics & Genomic Medicine
Background Gene therapy offers an etiologically targeted treatment for genetic disorders. Little is known about the acceptance of mortality risk among patients with progressive, fatal conditions. We assessed patients’ and caregivers’ maximum acce
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::94bcb1cf2f3fd1bd0687ccd08729b826
https://doaj.org/article/52d96db984d645b4b1d2e956eedbd260
https://doaj.org/article/52d96db984d645b4b1d2e956eedbd260
Akademický článek
Tento výsledek nelze pro nepřihlášené uživatele zobrazit.
K zobrazení výsledku je třeba se přihlásit.
K zobrazení výsledku je třeba se přihlásit.
Autor:
Valeria Ricotti, Alesia Sadosky, Ryan S. Paquin, Amy Strong Martin, Ryan Fischer, Holly L. Peay, Annie Ganot, Leo Russo, Katherine Beaverson, Edward C. Smith, Carl Morris, Colin Rensch, Carol Mansfield, Brennan Mange
Publikováno v:
Orphanet Journal of Rare Diseases
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-9 (2019)
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-9 (2019)
Purpose Several gene therapy trials for Duchenne muscular dystrophy initiated in 2018. Trial decision making is complicated by non-curative, time-limited benefits; the progressive, fatal course; and high unmet needs. Here, caregivers and patients pri
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5c0e13bc91fea98263f952b45995f213
https://pubmed.ncbi.nlm.nih.gov/31072340
https://pubmed.ncbi.nlm.nih.gov/31072340
Akademický článek
Tento výsledek nelze pro nepřihlášené uživatele zobrazit.
K zobrazení výsledku je třeba se přihlásit.
K zobrazení výsledku je třeba se přihlásit.