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pro vyhledávání: '"Alice Harmois"'
Autor:
Marcel Garcia, Morgane Daurat, Alain Morère, Marc Perez, Alice Harmois, Marie Maynadier, Afitz Da Silva, Khaled El Cheikh, Catherine Caillaud, Ilaria Basile, Bernard Pau, Magali Gary-Bobo, Henry-Vincent Charbonné, Anastasia Godefroy
Publikováno v:
Journal of Controlled Release
Journal of Controlled Release, Elsevier, 2018, 269, pp.15-23. ⟨10.1016/j.jconrel.2017.10.043⟩
Journal of Controlled Release, Elsevier, 2018, 269, pp.15-23. ⟨10.1016/j.jconrel.2017.10.043⟩
Pompe disease is a rare disorder due to deficiency of the acid a-glucosidase (GAA) treated by enzyme replacement therapy. The present authorized treatment with rhGAA, the recombinant human enzyme, provides an important benefit in the infantile onset;
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6dcbca864b4ea11ed8d8c1f95a3c6400
https://hal.archives-ouvertes.fr/hal-01837837
https://hal.archives-ouvertes.fr/hal-01837837
