Zobrazeno 1 - 10
of 98
pro vyhledávání: '"Alan L. Shields"'
Autor:
Alan L. Shields, Fiona Taylor, Roger E. Lamoureux, Brad Padilla, Kas Severson, Tanya Green, Anthony L. Boral, Cem Akin, Frank Siebenhaar, Brenton Mar
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 18, Iss 1, Pp 1-11 (2023)
Abstract Background The Indolent Systemic Mastocytosis Symptom Assessment Form (ISM-SAF) (©Blueprint Medicines Corporation), a 12-item daily diary that assesses 11 signs and symptoms of indolent systemic mastocytosis (ISM) and smoldering systemic ma
Externí odkaz:
https://doaj.org/article/94b4b613e6f74b538a3b3852443317a6
Autor:
Chad Gwaltney, Jonathan Stokes, Anthony Aiudi, Iyar Mazar, Sarah Ollis, Emily Love, Amel Karaa, Carrie R. Houts, R. J. Wirth, Alan L. Shields
Publikováno v:
Journal of Patient-Reported Outcomes, Vol 6, Iss 1, Pp 1-17 (2022)
Abstract Background The Primary Mitochondrial Myopathy Symptom Assessment (PMMSA) is a 10-item patient-reported outcome (PRO) measure designed to assess the severity of mitochondrial disease symptoms. Analyses of data from a clinical trial with PMM p
Externí odkaz:
https://doaj.org/article/8c98636a0cae452caf7677e0e2713dfd
Autor:
Fiona Taylor, Cem Akin, Roger E. Lamoureux, Brad Padilla, Tanya Green, Anthony L. Boral, Iyar Mazar, Brenton Mar, Alan L. Shields, Frank Siebenhaar
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-12 (2021)
Abstract Background Advanced systemic mastocytosis (AdvSM), indolent systemic mastocytosis (ISM), and smoldering systemic mastocytosis (SSM) are rare diseases characterized by neoplastic mast cell infiltration of more than one organ. A content-valid
Externí odkaz:
https://doaj.org/article/e7491e39c049481e9d007aca4e635049
Autor:
Brad Padilla, Alan L. Shields, Fiona Taylor, Xiaoran Li, Jeffrey Mcdonald, Tanya Green, Anthony L. Boral, Hui-Min Lin, Cem Akin, Frank Siebenhaar, Brenton Mar
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-10 (2021)
Abstract Background Indolent systemic mastocytosis (ISM) is a rare, clonal mast cell neoplasm characterized by severe, unpredictable symptoms. The Indolent Systemic Mastocytosis Symptom Assessment Form (ISM-SAF) items compose a Total Symptom Score (T
Externí odkaz:
https://doaj.org/article/f99dc0e48e5b4368acd4c26be63b00b4
Autor:
Iyar Mazar, Jonathan Stokes, Sarah Ollis, Emily Love, Ashlee Espensen, Peter G. Barth, John H. Powers, Alan L. Shields
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-8 (2019)
Abstract Background Barth syndrome (BTHS, OMIM 302060) is a rare, life-threatening, x-linked genetic disorder that occurs almost exclusively in males and is characterized by cardiomyopathy, neutropenia, skeletal muscle myopathy primarily affecting la
Externí odkaz:
https://doaj.org/article/b8086c2c7af8476fbc352a104b80e760
Autor:
Ruben A. Mesa, Yun Su, Adrien Woolfson, Josef T. Prchal, Kathleen Turnbull, Elias Jabbour, Robyn Scherber, Alan L. Shields, Meaghan Krohe, Funke Ojo, Farrah Pompilus, Joseph C. Cappelleri, Claire Harrison
Publikováno v:
Health and Quality of Life Outcomes, Vol 17, Iss 1, Pp 1-16 (2019)
Abstract Background The goal of the research reported here was to understand the patient experience of living with myelofibrosis (MF) and establish content validity of the Modified Myeloproliferative Neoplasm Symptom Assessment Diary (MPN-SD). Method
Externí odkaz:
https://doaj.org/article/10037569fd8641a283e259003be29fc8
Publikováno v:
Journal of Dermatological Treatment, Vol 29, Iss 2, Pp 152-164 (2018)
Background: Two patient-reported outcome (PRO) questionnaires, the Hidradenitis Suppurativa Symptom Assessment (HSSA) and Hidradenitis Suppurativa Impact Assessment (HSIA), were developed to measure signs, symptoms and impacts of HS in treatment effi
Externí odkaz:
https://doaj.org/article/0504beb5e0414bf8a79196fa9a6c822f
Autor:
April W. Armstrong, Benjamin Banderas, Catherine Foley, Jonathan Stokes, Murali Sundaram, Alan L. Shields
Publikováno v:
Journal of Dermatological Treatment, Vol 28, Iss 6, Pp 505-514 (2017)
Objective: The Self-Assessment of Psoriasis Symptoms – Clinical Trials (SAPS-CT) and SAPS – Real World (SAPS-RW) were simultaneously created to assess the experience of plaque psoriasis in two unique contexts. Methods: Qualitative and quantitativ
Externí odkaz:
https://doaj.org/article/49b1aba40f124770a9a45fb3356f6d80
Autor:
Meaghan Krohe, Yanni Hao, Roger E. Lamoureux, Nina Galipeau, Denise Globe, Catherine Foley, Iyar Mazar, Jeffrey Solomon, Alan L. Shields
Publikováno v:
Breast Cancer: Basic and Clinical Research, Vol 2016, Iss 10, Pp 93-102 (2016)
Externí odkaz:
https://doaj.org/article/81a2de5e6d694135a6b56673a232b746
Publikováno v:
Journal of Health Economics and Outcomes Research
**Background:** Among several factors that impair adherence to available therapies in type 2 diabetes mellitus (T2DM) is the complexity of the dosing regimen. Moreover, the value of a once-weekly (QW) administration of oral medications for T2DM compa
Externí odkaz:
https://doaj.org/article/3756cee30c2346c3bdca8b56045132dd