Allele-Specific Inhibition of Rhodopsin With an Antisense Oligonucleotide Slows Photoreceptor Cell Degeneration.

Autor: Murray SF; Isis Pharmaceuticals Carlsbad, California, United States., Jazayeri A; Isis Pharmaceuticals Carlsbad, California, United States., Matthes MT; University of California at San Francisco School of Medicine, Beckman Vision Center, San Francisco, California, United States., Yasumura D; University of California at San Francisco School of Medicine, Beckman Vision Center, San Francisco, California, United States., Yang H; University of California at San Francisco School of Medicine, Beckman Vision Center, San Francisco, California, United States., Peralta R; Isis Pharmaceuticals Carlsbad, California, United States., Watt A; Isis Pharmaceuticals Carlsbad, California, United States., Freier S; Isis Pharmaceuticals Carlsbad, California, United States., Hung G; Isis Pharmaceuticals Carlsbad, California, United States., Adamson PS; GlaxoSmithKlein, Brentford, Middlesex, United Kingdom., Guo S; Isis Pharmaceuticals Carlsbad, California, United States., Monia BP; Isis Pharmaceuticals Carlsbad, California, United States., LaVail MM; University of California at San Francisco School of Medicine, Beckman Vision Center, San Francisco, California, United States., McCaleb ML; Isis Pharmaceuticals Carlsbad, California, United States.

Publikováno v: Investigative ophthalmology & visual science [Invest Ophthalmol Vis Sci] 2015 Oct; Vol. 56 (11), pp. 6362-75.