Zobrazeno 1 - 3
of 3
pro vyhledávání: '"Furlong, Pat"'
Autor:
Kakkis ED; EveryLife Foundation for Rare Diseases, Novato, CA, USA. ekakkis@everylifefoundation.org., O'Donovan M; BioMarin Pharmaceutical Inc., Novato, CA, USA. modonovan@bmrn.com., Cox G; Genzyme Corporation, Cambridge, MA, USA. gerald.cox@genzyme.com., Hayes M; Synageva BioPharma Corp., Lexington, MA, USA. mark.hayes@synageva.com., Goodsaid F; Vertex Pharmaceuticals, Cambridge, MA, USA. federico_goodsaid@vrtx.com., Tandon PK; Genzyme Corporation, Cambridge, MA, USA. pk.tandon@genzyme.com., Furlong P; Parent Project Muscular Dystrophy, Middletown, OH, USA. pat@parentprojectmd.org., Boynton S; Shire, Lexington, MA, USA. sboynton@shire.com., Bozic M; Shire, Lexington, MA, USA. mbozic@shire.com., Orfali M; Pfizer Inc., Cambridge, MA, USA. may.orfali@pfizer.com., Thornton M; Sarcoma Foundation of America, Damascus, MD, USA. mthornton@curesarcoma.org.
Publikováno v:
Orphanet journal of rare diseases [Orphanet J Rare Dis] 2015 Feb 10; Vol. 10, pp. 16. Date of Electronic Publication: 2015 Feb 10.
Autor:
Victor, Ronald G, Sweeney, H. Lee, Finkel, Richard, Mcdonald, Craig M, Byrne, Barry, Eagle, Michelle, Goemans, Nathalie, Vandenborne, Krista, Dubrovsky, Alberto L, Topaloglu, Haluk, Miceli, M. Carrie, Furlong, Pat, Landry, John, Elashoff, Robert, Cox, David, Hoda, Abdel-Hamid, Susan, Apkon, Richard, Barohn, Elena, Belousova, Enrico, Bertini, John, Brandsema, Claudio, Bruno, William, Burnette, Russell, Butterfield, Barry, Byrne, Craig, Campbell, Jose, Carlo, Jong-Hee, Chae, Saleel, Chandratre, Giacomo, Comi, Anne, Connolly, Imelda De Groot, Nicolas, Deconinck, Joseph, Dooley, Alberto, Dubrovsky, Julien, Durigneux, Erika, Finanger, Richard, Finkel, L Matthew Frank, Nathalie, Goemans, Amy, Harper, Ayako, Hattori, Ozlem, Herguner, Susan, Iannaccone, Joanne, Janas, Yuh-Jyh, Jong, Janberd, Kirschner, Hirofumi, Komaki, Nancy, Kuntz, Wang-Tso, Lee, Edward, Leung, Jean, Mah, Katherine, Mathews, Craig, Mcdonald, Eugenio, Mercuri, Hugh, Mcmillan, Wolfgang, Mueller-Felber, Adolfo Lopez de Munain, Akinori, Nakamura, Erik, Niks, Katsuhisa, Ogata, Samuel, Pascual, Pegoraro, Elena, Yann, Pereon, Ben, Renfroe, Ratna Bhavaraju Sanka, Jens, Schallner, Ulrike, Schara, Kathryn, Selby, Isabel Illa Sendra, Laurent, Servais, Edward, Smith, Susan, Sparks, Haluk, Topaloglu, Ron, Victor, Juan Jose Vilchez, Matthew, Wicklund, Ekkehard, Wilichoswki, Brenda, Wong
Publikováno v:
Neurology, vol 89, iss 17
Neurology
Neurology, 89(17), 1811-1820
Neurology, 89 (17
Neurology
Neurology, 89(17), 1811-1820
Neurology, 89 (17
To conduct a randomized trial to test the primary hypothesis that once-daily tadalafil, administered orally for 48 weeks, lessens the decline in ambulatory ability in boys with Duchenne muscular dystrophy (DMD).
info:eu-repo/semantics/published
info:eu-repo/semantics/published
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6e0e6503a882dfb553f43c58e0475c30
https://ora.ox.ac.uk/objects/uuid:07acefc6-f3c1-43d6-aaff-dd314f53221c
https://ora.ox.ac.uk/objects/uuid:07acefc6-f3c1-43d6-aaff-dd314f53221c
Autor:
Straub, Volker1, Balabanov, Pavel2, Bushby, Kate1, Ensini, Monica1, Goemans, Nathalie3, De Luca, Annamaria4, Pereda, Alejandra5, Hemmings, Robert6, Campion, Giles7, Kaye, Edward8, Arechavala-Gomeza, Virginia9, Goyenvalle, Aurelie10, Niks, Erik11, Veldhuizen, Olav1, Furlong, Pat12, Stoyanova-Beninska, Violeta13, Wood, Matthew J14, Johnson, Alex15, Mercuri, Eugenio16, Muntoni, Francesco17
Publikováno v:
Lancet Neurology. Jul2016, Vol. 15 Issue 8, p882-890. 9p.