Zobrazeno 1 - 2
of 2
pro vyhledávání: '"Furlong, Pat"'
Autor:
Furlong, Pat1, Bridges, John F. P.2, Charnas, Lawrence3, Fallon, Justin R.4, Fischer, Ryan1, Flanigan, Kevin M.5, Franson, Timothy R.6, Gulati, Neera7, McDonald, Craig8, Peay, Holly1 Pat@parentprojectmd.org, Lee Sweeney, H.9
Publikováno v:
Orphanet Journal of Rare Diseases. Jul2015, Vol. 10 Issue 1, p1-9. 9p.
Autor:
Larkindale, Jane, Abresch, Richard, Aviles, Enrique, Bronson, Abby, Chin, Janice, Furlong, Pat, Gordish-Dressman, Heather, Habeeb-Louks, Elizabeth, Henricson, Erik, Kroger, Hans, Lynn, Charles, Lynn, Stephen, Martin, Dana, Nuckolls, Glen, Rooney, William, Romero, Klaus, Sweeney, Lee, Vandenborne, Krista, Walter, Glenn, Wolff, Jodi, Wong, Brenda, McDonald, Craig M., Duchenne Regulatory Science Consortium, Imaging-DMD Consortium and the CINRG Investigators, members of the
Publikováno v:
PLoS Currents
Introduction: The Duchenne Regulatory Science Consortium (D-RSC) was established to develop tools to accelerate drug development for DMD. The resulting tools are anticipated to meet validity requirements outlined by qualification/endorsement pathways