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pro vyhledávání: '"Jessica Summers"'
Autor:
Nermina Ferizovic, Jessica Summers, Igor Beitia Ortiz de Zárate, Christian Werner, Joel Jiang, Erik Landfeldt, Katharina Buesch
Publikováno v:
PLoS ONE, Vol 17, Iss 3, p e0265879 (2022)
BackgroundDuchenne muscular dystrophy (DMD) is a rare, severely debilitating, and fatal neuromuscular disease characterized by progressive muscle degeneration. Like in many orphan diseases, randomized controlled trials are uncommon in DMD, resulting
Externí odkaz:
https://doaj.org/article/40ec53f8b01e432d9568f6f2553a52f2