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of 16 326
pro vyhledávání: ''
Autor:
Mahlangu, Johnny, Kaczmarek, Radoslaw, von Drygalski, Annette, Shapiro, Susan, Chou, Sheng-Chieh, Ozelo, Margareth C, Kenet, Gili, Peyvandi, Flora, Wang, Michael, Madan, Bella, Key, Nigel S, Laffan, Michael, Dunn, Amy L, Mason, Jane, Quon, Doris V, Symington, Emily, Leavitt, Andrew D, Oldenburg, Johannes, Chambost, Hervé, Reding, Mark T, Jayaram, Kala, Yu, Hua, Mahajan, Reena, Chavele, Konstantia-Maria, Reddy, Divya B, Henshaw, Joshua, Robinson, Tara M, Wong, Wing Yen, Pipe, Steven W, GENEr8-1 Trial Group, Hermans, Cédric
Publikováno v:
The New England journal of medicine, Vol. 388, no.8, p. 694-705 (2023)
BACKGROUND: Valoctocogene roxaparvovec delivers a B-domain-deleted factor VIII coding sequence with an adeno-associated virus vector to prevent bleeding in persons with severe hemophilia A. The findings of a phase 3 study of the efficacy and safety o
Autor:
Robert L, Glicksman
Publikováno v:
New England Journal of Medicine. 388:84-88
Publikováno v:
New England Journal of Medicine. 387:2436-2448
Autor:
Howard BUNN
Publikováno v:
New England Journal of Medicine. 387:2362-2365
Autor:
Peter B, Gilbert, Ruben O, Donis, Richard A, Koup, Youyi, Fong, Stanley A, Plotkin, Dean, Follmann
Publikováno v:
New England Journal of Medicine. 387:2203-2206
Publikováno v:
New England Journal of Medicine. 387:2269-2277
Autor:
Shireen V. Guide, Mercedes E. Gonzalez, I. Sinem Bağcı, Brittani Agostini, Hubert Chen, Gloria Feeney, Molly Steimer, Binoy Kapadia, Kunju Sridhar, Lori Quesada Sanchez, Franshesca Gonzalez, Matthew Van Ligten, Trevor J. Parry, Surya Chitra, Lisa A. Kammerman, Suma Krishnan, M. Peter Marinkovich
Publikováno v:
New England Journal of Medicine. 387:2211-2219
Dystrophic epidermolysis bullosa is a rare genetic blistering skin disease caused by mutations inWe conducted a phase 3, double-blind, intrapatient randomized, placebo-controlled trial involving patients 6 months of age or older with genetically conf
Autor:
Matthew B. Roberts, Jarone Lee, Mark C. Murphy, Arthur Y. Kim, Erin E. Coglianese, Caroline Hilburn
Publikováno v:
New England Journal of Medicine. 387:2172-2183
Autor:
John Olynyk, Grant Ramm
Publikováno v:
New England Journal of Medicine. 387:2159-2170
Autor:
Kevin D, Hill, Prince J, Kannankeril, Jeffrey P, Jacobs, H Scott, Baldwin, Marshall L, Jacobs, Sean M, O'Brien, David P, Bichel, Eric M, Graham, Brian, Blasiole, Ashraf, Resheidat, Adil S, Husain, S Ram, Kumar, Jerry L, Kirchner, Dianne S, Gallup, Joseph W, Turek, Mark, Bleiweis, Bret, Mettler, Alexis, Benscoter, Eric, Wald, Tara, Karamlou, Andrew H, Van Bergen, David, Overman, Pirooz, Eghtesady, Ryan, Butts, John S, Kim, John P, Scott, Brett R, Anderson, Michael F, Swartz, Patrick I, McConnell, David F, Vener, Jennifer S, Li, Kimberly, Teknipp
Publikováno v:
N Engl J Med
BACKGROUND: Although perioperative prophylactic glucocorticoids have been used for decades, whether they improve outcomes in infants after heart surgery with cardiopulmonary bypass is unknown. METHODS: We conducted a multicenter, prospective, randomi