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pro vyhledávání: '"Tahseen Mozaffar"'
Autor:
Tahseen Mozaffar, Lionel Riou França, Jérôme Msihid, Pragya Shukla, Irina Proskorovsky, Tianyue Zhou, Magali Periquet, Kristina An Haack, Laurence Pollissard, Volker Straub
Publikováno v:
Molecular Genetics and Metabolism Reports, Vol 40, Iss , Pp 101109- (2024)
Background: The efficacy of avalglucosidase alfa (AVA) versus alglucosidase alfa (ALG) on forced vital capacity percent predicted (FVCpp) in patients with late-onset Pompe disease (LOPD) has been assessed in the Phase 3 COMET trial (NCT02782741). Due
Externí odkaz:
https://doaj.org/article/8c1269ee7f074a86a443bd3cdd49e43a