Zobrazeno 1 - 1
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pro vyhledávání: '"Olimpia Musumeci"'
Publikováno v:
Behavioral Sciences, Vol 13, Iss 12, p 956 (2023)
Pompe disease (PD) is a rare metabolic disorder with progressive neuromuscular consequences that negatively impact a child’s development and quality of life (QoL). Despite an improved prognosis with treatment, the risk for early death due cardiores
Externí odkaz:
https://doaj.org/article/ac87164bca2f4bc89618da5e266abb51