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Autor:
Fridman V; Department of Neurology, University of Colorado Denver, Aurora, CO, USA., Sillau S; Department of Neurology, University of Colorado Denver, Aurora, CO, USA., Bockhorst J; Department of Neurology, University of Colorado Denver, Aurora, CO, USA., Smith K; Department of Neurology, University of Colorado Denver, Aurora, CO, USA., Moroni I; Department of Child Neurology, Scientific Institute for Research and Health Care Foundation Carlo Besta Neurological Institute, Milan, Italy., Pagliano E; Department of Child Neurology, Scientific Institute for Research and Health Care Foundation Carlo Besta Neurological Institute, Milan, Italy., Pisciotta C; Department of Clinical Neurosciences, Scientific Institute for Research and Health Care Foundation Carlo Besta Neurological Institute, Milan, Italy., Piscosquito G; Department of Clinical Neurosciences, Scientific Institute for Research and Health Care Foundation Carlo Besta Neurological Institute, Milan, Italy.; Maugeri Scientific Clinical Institutes, Neurorehabilitation Unit, Scientific Institute of Telese Terme, Telese Terme, Italy., Laurá M; Centre for Neuromuscular Diseases, University College London Queen Square Institute of Neurology, London, UK., Muntoni F; Dubowitz Neuromuscular Centre, University College London Institute of Child Health and Great Ormond Street Hospital, London, UK., Bacon C; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA., Feely S; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA.; Department of Neurology, Wayne State University, Detroit, MI, USA., Grider T; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA., Gutmann L; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA., Shy R; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA.; Department of Neurology, Wayne State University, Detroit, MI, USA., Wilcox J; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA., Herrmann DN; Department of Neurology, University of Rochester, Rochester, NY, USA., Li J; Department of Neurology, Wayne State University, Detroit, MI, USA.; Department of Neurology, Vanderbilt University, Nashville, TN, USA., Ramchandren S; Department of Neurology, Wayne State University, Detroit, MI, USA.; Department of Neurology, University of Michigan, Ann Arbor, MI, USA.; PRA Health Sciences, Raleigh, NC, USA., Sumner CJ; Departments of Neurology and Neuroscience, John Hopkins University School of Medicine, Baltimore, MD, USA., Lloyd TE; Departments of Neurology and Neuroscience, John Hopkins University School of Medicine, Baltimore, MD, USA., Day J; Department of Neurology, Stanford University, Stanford, CA, USA., Siskind CE; Department of Neurology, Stanford University, Stanford, CA, USA., Yum SW; Department of Neurology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.; Department of Neurology, Children's Hospital of Philadelphia, Philadelphia, PA, USA., Sadjadi R; Department of Neurology, Massachusetts General Hospital, Boston, MA, USA., Finkel RS; Department of Neurology, Nemours Children's Hospital, Orlando, FL, USA., Scherer SS; Department of Neurology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Pareyson D; Department of Clinical Neurosciences, Scientific Institute for Research and Health Care Foundation Carlo Besta Neurological Institute, Milan, Italy., Reilly MM; Centre for Neuromuscular Diseases, University College London Queen Square Institute of Neurology, London, UK., Shy ME; Department of Neurology, University of Iowa Hospitals and Clinics, Iowa City, IA, USA.; Department of Neurology, Wayne State University, Detroit, MI, USA.
Publikováno v:
Annals of neurology [Ann Neurol] 2023 Mar; Vol. 93 (3), pp. 563-576. Date of Electronic Publication: 2022 Oct 28.